Phuturdex › Listed companies
Companies listed in the US · updated 13 November 2026
Companies listed in the US
Data from official sources, not financial advice.
367 companies listed in the United States (exchange and ticker from SEC EDGAR) that sponsor active clinical trials, with their pipeline by phase, upcoming dates and SEC data, updated 13 November 2026.
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Preview: 367 listed companies. Sign up for free to search all 8,346 drugs and 30,697 trials, with filters, email alerts, PDF and Excel.
Get free access →Companies with the most drugs in development
- AstraZeneca NYSE: AZN · 181 drugs
- Eli Lilly and Company NYSE: LLY · 144 drugs
- AbbVie NYSE: ABBV · 116 drugs
- Bristol-Myers Squibb NYSE: BMY · 109 drugs
- Pfizer NYSE: PFE · 108 drugs
- Regeneron Pharmaceuticals Nasdaq: REGN · 77 drugs
- Sanofi Nasdaq: SNY · 75 drugs
- Amgen Nasdaq: AMGN · 55 drugs
- BeOne Medicines Nasdaq: ONC · 53 drugs
- Gilead Sciences Nasdaq: GILD · 51 drugs
- Incyte Corporation Nasdaq: INCY · 41 drugs
- Novo Nordisk A/S NYSE: NVO · 39 drugs
- Genmab Nasdaq: GMAB · 38 drugs
- BioNTech SE Nasdaq: BNTX · 37 drugs
- Jazz Pharmaceuticals Nasdaq: JAZZ · 25 drugs
- Exelixis Nasdaq: EXEL · 21 drugs
- Revolution Medicines, Inc. Nasdaq: RVMD · 19 drugs
- ImmunityBio, Inc. Nasdaq: IBRX · 18 drugs
- Karyopharm Therapeutics Inc Nasdaq: KPTI · 18 drugs
- Biogen Nasdaq: BIIB · 16 drugs
- Kura Oncology, Inc. Nasdaq: KURA · 16 drugs
- Inhibrx Biosciences, Inc Nasdaq: INBX · 15 drugs
- Alnylam Pharmaceuticals Nasdaq: ALNY · 14 drugs
- IDEAYA Biosciences Nasdaq: IDYA · 14 drugs
All companies (A–Z)
- 4D Molecular Therapeutics Nasdaq: FDMT · 3 drugs
- 60 Degrees Pharmaceuticals LLC Nasdaq: SXTP · 1 drug
- AbbVie NYSE: ABBV · 116 drugs
- AbCellera Biologics Inc. Nasdaq: ABCL · 2 drugs
- Abeona Therapeutics, Inc Nasdaq: ABEO · 1 drug
- Abivax S.A. Nasdaq: ABVX · 1 drug
- AC Immune SA Nasdaq: ACIU · 1 drug
- ACADIA Pharmaceuticals Inc. Nasdaq: ACAD · 2 drugs
- Achieve Life Sciences Nasdaq: ACHV · 1 drug
- Aclaris Therapeutics, Inc. Nasdaq: ACRS · 1 drug
- Acrivon Therapeutics Nasdaq: ACRV · 3 drugs
- Actinium Pharmaceuticals NYSE: ATNM · 3 drugs
- Actuate Therapeutics Inc. Nasdaq: ACTU · 7 drugs
- Acumen Pharmaceuticals Nasdaq: ABOS · 1 drug
- Acurx Pharmaceuticals Inc. Nasdaq: ACXP · 1 drug
- Adagene Inc Nasdaq: ADAG · 3 drugs
- ADARx Pharmaceuticals, Inc. Nasdaq: ADRX · 5 drugs
- ADC Therapeutics S.A. NYSE: ADCT · 6 drugs
- Agenus Inc. Nasdaq: AGEN · 2 drugs
- Agios Pharmaceuticals, Inc. Nasdaq: AGIO · 4 drugs
- Akebia Therapeutics Nasdaq: AKBA · 3 drugs
- Aligos Therapeutics Nasdaq: ALGS · 3 drugs
- Alkermes, Inc. Nasdaq: ALKS · 2 drugs
- Allarity Therapeutics Nasdaq: ALLR · 1 drug
- Allogene Therapeutics Nasdaq: ALLO · 6 drugs
- Alnylam Pharmaceuticals Nasdaq: ALNY · 14 drugs
- Alterity Therapeutics Nasdaq: ATHE · 1 drug
- Altimmune, Inc. Nasdaq: ALT · 1 drug
- Alto Neuroscience NYSE: ANRO · 4 drugs
- Alumis Inc Nasdaq: ALMS · 1 drug
- Alzamend Neuro, Inc. Nasdaq: ALZN · 3 drugs
- Amgen Nasdaq: AMGN · 55 drugs
- Amneal Pharmaceuticals, LLC Nasdaq: AMRX · 1 drug
- Amylyx Pharmaceuticals Inc. Nasdaq: AMLX · 3 drugs
- AN2 Therapeutics, Inc Nasdaq: ANTX · 1 drug
- AnaptysBio, Inc. Nasdaq: ANAB · 1 drug
- Annexon, Inc. Nasdaq: ANNX · 1 drug
- Annovis Bio Inc. NYSE: ANVS · 2 drugs
- Apnimed Nasdaq: APMD · 2 drugs
- Apollomics Inc. Nasdaq: APLM · 1 drug
- Aprea Therapeutics Nasdaq: APRE · 1 drug
- Aptevo Therapeutics Nasdaq: APVO · 3 drugs
- Arcus Biosciences, Inc. NYSE: RCUS · 12 drugs
- Arcutis Biotherapeutics, Inc. Nasdaq: ARQT · 2 drugs
- Ardelyx Nasdaq: ARDX · 1 drug
- argenx Nasdaq: ARGX · 5 drugs
- ArriVent BioPharma, Inc. Nasdaq: AVBP · 4 drugs
- Arrowhead Pharmaceuticals Nasdaq: ARWR · 4 drugs
- ARS Pharmaceuticals, Inc. Nasdaq: SPRY · 1 drug
- Artiva Biotherapeutics, Inc. Nasdaq: ARTV · 5 drugs
- Arvinas Inc. Nasdaq: ARVN · 5 drugs
- Ascendis Pharma A/S Nasdaq: ASND · 3 drugs
- Aspen Neuroscience Nasdaq: ASPE · 1 drug
- Assembly Biosciences Nasdaq: ASMB · 1 drug
- AstraZeneca NYSE: AZN · 181 drugs
- Atea Pharmaceuticals, Inc. Nasdaq: AVIR · 1 drug
- Atossa Therapeutics, Inc. Nasdaq: ATOS · 2 drugs
- Atrium Therapeutics Nasdaq: RNA · 1 drug
- Attovia Therapeutics Inc Nasdaq: ATTO · 2 drugs
- aTyr Pharma, Inc. Nasdaq: ATYR · 1 drug
- Aurinia Pharmaceuticals Inc. Nasdaq: AUPH · 1 drug
- Avalyn Pharma Inc. Nasdaq: AVLN · 2 drugs
- Axsome Therapeutics, Inc. Nasdaq: AXSM · 4 drugs
- Azitra Inc. NYSE: AZTR · 1 drug
- Bambusa Therapeutics Nasdaq: BBTX · 2 drugs
- Bausch & Lomb Incorporated NYSE: BLCO · 1 drug
- Beam Therapeutics Inc. Nasdaq: BEAM · 4 drugs
- Belite Bio, Inc Nasdaq: BLTE · 1 drug
- BeOne Medicines Nasdaq: ONC · 53 drugs
- Bicara Therapeutics Nasdaq: BCAX · 2 drugs
- BioAge Labs, Inc. Nasdaq: BIOA · 1 drug
- BioCryst Pharmaceuticals Nasdaq: BCRX · 2 drugs
- Biogen Nasdaq: BIIB · 16 drugs
- BioLineRx, Ltd. Nasdaq: BLRX · 1 drug
- BioMarin Pharmaceutical Nasdaq: BMRN · 7 drugs
- Biomea Fusion Inc. Nasdaq: BMEA · 1 drug
- BioNTech SE Nasdaq: BNTX · 37 drugs
- BioRestorative Therapies Nasdaq: BRTX · 1 drug
- Bioventus LLC Nasdaq: BVS · 1 drug
- Black Diamond Therapeutics, Inc. Nasdaq: BDTX · 2 drugs
- BlossomHill Therapeutics Nasdaq: BLSM · 5 drugs
- Bolt Biotherapeutics, Inc. Nasdaq: BOLT · 1 drug
- Braveheart Bio, Inc. Nasdaq: BRVE · 1 drug
- BriaCell Therapeutics Corporation Nasdaq: BCTX · 2 drugs
- Bright Minds Biosciences Pty Ltd Nasdaq: DRUG · 1 drug
- Bristol-Myers Squibb NYSE: BMY · 109 drugs
- C4 Therapeutics, Inc. Nasdaq: CCCC · 3 drugs
- Cabaletta Bio Nasdaq: CABA · 3 drugs
- CAMP4 Therapeutics Corporation Nasdaq: CAMP · 1 drug
- Can-Fite BioPharma NYSE: CANF · 2 drugs
- Candel Therapeutics, Inc. Nasdaq: CADL · 2 drugs
- Cardiff Oncology Nasdaq: CRDF · 2 drugs
- Cardiol Therapeutics Inc. Nasdaq: CRDL · 1 drug
- Caribou Biosciences, Inc. Nasdaq: CRBU · 4 drugs
- Cartesian Therapeutics Nasdaq: RNAC · 2 drugs
- Celcuity Inc Nasdaq: CELC · 5 drugs
- Celldex Therapeutics Nasdaq: CLDX · 2 drugs
- Cellectar Biosciences, Inc. Nasdaq: CLRB · 2 drugs
- Cellectis S.A. Nasdaq: CLLS · 4 drugs
- Century Therapeutics, Inc. Nasdaq: IPSC · 1 drug
- Clearmind Medicine Inc. Nasdaq: CMND · 1 drug
- Climb Bio, Inc. Nasdaq: CLYM · 2 drugs
- CNS Pharmaceuticals, Inc. Nasdaq: CNSP · 1 drug
- Cogent Biosciences, Inc. Nasdaq: COGT · 6 drugs
- Cognition Therapeutics Nasdaq: CGTX · 1 drug
- Coherus Oncology, Inc. Nasdaq: CHRS · 7 drugs
- Colgate Palmolive NYSE: CL · 1 drug
- COMPASS Pathways Nasdaq: CMPS · 1 drug
- Compass Therapeutics Nasdaq: CMPX · 5 drugs
- Compugen Ltd Nasdaq: CGEN · 3 drugs
- Context Therapeutics Inc. Nasdaq: CNTX · 2 drugs
- Contineum Therapeutics Nasdaq: CTNM · 1 drug
- Corcept Therapeutics Nasdaq: CORT · 7 drugs
- Corvus Pharmaceuticals, Inc. Nasdaq: CRVS · 1 drug
- Coya Therapeutics Nasdaq: COYA · 1 drug
- Creative Medical Technology Holdings Inc Nasdaq: CELZ · 1 drug
- Crescent Biopharma, Inc. Nasdaq: CBIO · 11 drugs
- CRISPR Therapeutics Nasdaq: CRSP · 4 drugs
- Cullinan Therapeutics Inc. Nasdaq: CGEM · 10 drugs
- Cumberland Pharmaceuticals Nasdaq: CPIX · 1 drug
- Curis, Inc. Nasdaq: CRIS · 3 drugs
- Cytokinetics Nasdaq: CYTK · 3 drugs
- CytomX Therapeutics Nasdaq: CTMX · 5 drugs
- Damora Therapeutics Nasdaq: DMRA · 2 drugs
- DBV Technologies Nasdaq: DBVT · 1 drug
- Delcath Systems Inc. Nasdaq: DCTH · 5 drugs
- Denali Therapeutics Inc. Nasdaq: DNLI · 8 drugs
- Design Therapeutics, Inc. Nasdaq: DSGN · 2 drugs
- Disc Medicine, Inc Nasdaq: IRON · 3 drugs
- Dogwood Therapeutics Inc. Nasdaq: DWTX · 1 drug
- Dyne Therapeutics Nasdaq: DYN · 2 drugs
- Edesa Biotech Inc. Nasdaq: EDSA · 1 drug
- Edgewise Therapeutics, Inc. Nasdaq: EWTX · 3 drugs
- Editas Medicine, Inc. Nasdaq: EDIT · 1 drug
- Eikon Therapeutics Nasdaq: EIKN · 10 drugs
- Electra Therapeutics Inc. Nasdaq: ETRA · 1 drug
- Eledon Pharmaceuticals Nasdaq: ELDN · 1 drug
- Eli Lilly and Company NYSE: LLY · 144 drugs
- Eloxx Pharmaceuticals, Inc. Nasdaq: ELOX · 1 drug
- Enanta Pharmaceuticals, Inc Nasdaq: ENTA · 2 drugs
- Enliven Therapeutics Nasdaq: ELVN · 11 drugs
- Ensysce Biosciences Nasdaq: ENSC · 2 drugs
- Entrada Therapeutics, Inc. Nasdaq: TRDA · 2 drugs
- Equillium Nasdaq: EQ · 1 drug
- Erasca, Inc. Nasdaq: ERAS · 4 drugs
- Estrella Immunopharma, Inc. Nasdaq: ESLA · 1 drug
- Eupraxia Pharmaceuticals Inc. Nasdaq: EPRX · 1 drug
- Evommune, Inc. NYSE: EVMN · 1 drug
- Exelixis Nasdaq: EXEL · 21 drugs
- Faeth Therapeutics Nasdaq: FTH · 4 drugs
- Fate Therapeutics Nasdaq: FATE · 11 drugs
- FibroBiologics Nasdaq: FBLG · 1 drug
- Foghorn Therapeutics Inc. Nasdaq: FHTX · 3 drugs
- Gain Therapeutics, Inc. Nasdaq: GANX · 1 drug
- Galmed Pharmaceuticals Ltd Nasdaq: EOCN · 1 drug
- Genelux Corporation Nasdaq: GNLX · 11 drugs
- Generate Biomedicines Nasdaq: GENB · 5 drugs
- Genmab Nasdaq: GMAB · 38 drugs
- Genprex, Inc. Nasdaq: GNPX · 3 drugs
- Geron Corporation Nasdaq: GERN · 2 drugs
- Gilead Sciences Nasdaq: GILD · 51 drugs
- Glaukos Corporation NYSE: GKOS · 2 drugs
- Grace Therapeutics Inc. Nasdaq: GRCE · 1 drug
- Greenwich LifeSciences, Inc. Nasdaq: GLSI · 1 drug
- Halozyme Therapeutics Nasdaq: HALO · 1 drug
- HCW Biologics Nasdaq: HCWB · 1 drug
- Humacyte, Inc. Nasdaq: HUMA · 1 drug
- Iambic Therapeutics, Inc Nasdaq: IAM · 1 drug
- iBio, Inc. Nasdaq: IBIO · 2 drugs
- IDEAYA Biosciences Nasdaq: IDYA · 14 drugs
- Immuneering Corporation Nasdaq: IMRX · 5 drugs
- Immunic AG Nasdaq: IMUX · 1 drug
- ImmunityBio, Inc. Nasdaq: IBRX · 18 drugs
- Immunome, Inc. Nasdaq: IMNM · 5 drugs
- Immutep S.A.S. Nasdaq: IMMP · 6 drugs
- Imunon Nasdaq: IMNN · 6 drugs
- Incannex Healthcare Ltd Nasdaq: IXHL · 2 drugs
- Incyte Corporation Nasdaq: INCY · 41 drugs
- Indaptus Therapeutics, Inc Nasdaq: INDP · 2 drugs
- Inhibikase Therapeutics Nasdaq: IKT · 1 drug
- Inhibrx Biosciences, Inc Nasdaq: INBX · 15 drugs
- Innate Pharma Nasdaq: IPHA · 3 drugs
- Inovio Pharmaceuticals Nasdaq: INO · 4 drugs
- Insmed Incorporated Nasdaq: INSM · 4 drugs
- Intellia Therapeutics Nasdaq: NTLA · 2 drugs
- Intensity Therapeutics, Inc. Nasdaq: INTS · 1 drug
- Intuitive Surgical Nasdaq: ISRG · 1 drug
- Invivyd, Inc. Nasdaq: IVVD · 3 drugs
- Ionis Pharmaceuticals, Inc. Nasdaq: IONS · 12 drugs
- Iovance Biotherapeutics, Inc. Nasdaq: IOVA · 5 drugs
- IRulya Therapeutics Inc. Nasdaq: IRLA · 1 drug
- Jade Biosciences, Inc. Nasdaq: JBIO · 2 drugs
- Janux Therapeutics Nasdaq: JANX · 6 drugs
- Jazz Pharmaceuticals Nasdaq: JAZZ · 25 drugs
- Kardigan, Inc. Nasdaq: KARD · 3 drugs
- Karyopharm Therapeutics Inc Nasdaq: KPTI · 18 drugs
- Keros Therapeutics, Inc. Nasdaq: KROS · 1 drug
- Kiniksa Pharmaceuticals International, plc Nasdaq: KNSA · 1 drug
- Kiora Pharmaceuticals, Inc. Nasdaq: KPRX · 1 drug
- Kodiak Sciences Inc Nasdaq: KOD · 2 drugs
- Korro Bio, Inc. Nasdaq: KRRO · 1 drug
- Krystal Biotech, Inc. Nasdaq: KRYS · 11 drugs
- Kura Oncology, Inc. Nasdaq: KURA · 16 drugs
- Kymera Therapeutics, Inc. Nasdaq: KYMR · 1 drug
- Kyntra Bio Nasdaq: KYNB · 2 drugs
- Kyverna Therapeutics Nasdaq: KYTX · 1 drug
- Lantern Pharma Inc. Nasdaq: LTRN · 8 drugs
- Larimar Therapeutics, Inc. Nasdaq: LRMR · 1 drug
- Latigo Biotherapeutics Nasdaq: LTGO · 3 drugs
- LB Pharmaceuticals Inc. Nasdaq: LBRX · 1 drug
- LeonaBio Nasdaq: LONA · 2 drugs
- Lexeo Therapeutics Nasdaq: LXEO · 3 drugs
- Lexicon Pharmaceuticals Nasdaq: LXRX · 1 drug
- Lipocine Inc. Nasdaq: LPCN · 1 drug
- Lycia Therapeutics, Inc. Nasdaq: LYCA · 1 drug
- Lyell Immunopharma, Inc. Nasdaq: LYEL · 3 drugs
- MacroGenics Nasdaq: MGNX · 6 drugs
- Madrigal Pharmaceuticals, Inc. Nasdaq: MDGL · 1 drug
- Maia Biotechnology NYSE: MAIA · 2 drugs
- Mannkind Corporation Nasdaq: MNKD · 1 drug
- MapLight Therapeutics Nasdaq: MPLT · 2 drugs
- Marker Therapeutics, Inc. Nasdaq: MRKR · 2 drugs
- Maze Therapeutics Nasdaq: MAZE · 2 drugs
- MBX Biosciences Nasdaq: MBX · 2 drugs
- MediciNova Nasdaq: MNOV · 2 drugs
- MediWound Ltd Nasdaq: MDWD · 2 drugs
- Milestone Pharmaceuticals Inc. Nasdaq: MIST · 1 drug
- Mineralys Therapeutics Inc. Nasdaq: MLYS · 1 drug
- Minerva Neurosciences Nasdaq: NERV · 4 drugs
- MiNK Therapeutics Nasdaq: INKT · 1 drug
- Mirum Pharmaceuticals, Inc. Nasdaq: MIRM · 4 drugs
- Moleculin Biotech, Inc. Nasdaq: MBRX · 1 drug
- Monopar Therapeutics Nasdaq: MNPR · 1 drug
- Monte Rosa Therapeutics, Inc Nasdaq: GLUE · 3 drugs
- MoonLake Immunotherapeutics AG Nasdaq: MLTX · 1 drug
- Nanobiotix Nasdaq: NBTX · 3 drugs
- Nasus Pharma NYSE: NSRX · 2 drugs
- Nektar Therapeutics Nasdaq: NKTR · 1 drug
- NervGen Pharma Nasdaq: NGEN · 1 drug
- Neurocrine Biosciences Nasdaq: NBIX · 9 drugs
- Neurogene Inc. Nasdaq: NGNE · 2 drugs
- NewAmsterdam Pharma Nasdaq: NAMS · 3 drugs
- NextCure, Inc. Nasdaq: NXTC · 1 drug
- Nkarta, Inc. Nasdaq: NKTX · 4 drugs
- Novo Nordisk A/S NYSE: NVO · 39 drugs
- NovoCure GmbH Nasdaq: NVCR · 2 drugs
- NuCana plc Nasdaq: NCNA · 2 drugs
- Nurix Therapeutics, Inc. Nasdaq: NRIX · 8 drugs
- Nuvation Bio Inc. NYSE: NUVB · 4 drugs
- Nuvectis Pharma, Inc. Nasdaq: NVCT · 3 drugs
- Obsidian Therapeutics, Inc. Nasdaq: OBX · 1 drug
- Ocugen Nasdaq: OCGN · 4 drugs
- Ocular Therapeutix, Inc. Nasdaq: OCUL · 1 drug
- Odyssey Therapeutics, Inc. Nasdaq: ODTX · 3 drugs
- Olema Pharmaceuticals, Inc. Nasdaq: OLMA · 8 drugs
- Omeros Corporation Nasdaq: OMER · 1 drug
- Oncolytics Biotech Nasdaq: ONCY · 8 drugs
- OPKO Health, Inc. Nasdaq: OPK · 2 drugs
- Organon and Co NYSE: OGN · 1 drug
- ORIC Pharmaceuticals Nasdaq: ORIC · 8 drugs
- Oruka Therapeutics, Inc. Nasdaq: ORKA · 2 drugs
- Outlook Therapeutics, Inc. Nasdaq: OTLK · 1 drug
- Palatin Technologies, Inc Nasdaq: PTN · 3 drugs
- Palisade Bio Nasdaq: PALI · 1 drug
- Palvella Therapeutics, Inc. Nasdaq: PVLA · 1 drug
- Parabilis Medicines, Inc. Nasdaq: PBLS · 5 drugs
- Pasithea Therapeutics Corp. Nasdaq: KTTA · 1 drug
- Perspective Therapeutics NYSE: CATX · 3 drugs
- Pfizer NYSE: PFE · 108 drugs
- Phathom Pharmaceuticals, Inc. Nasdaq: PHAT · 1 drug
- Pliant Therapeutics, Inc. Nasdaq: PLRX · 2 drugs
- PMV Pharmaceuticals, Inc Nasdaq: PMVP · 6 drugs
- Polaryx Therapeutics, Inc. Nasdaq: PLYX · 1 drug
- Praxis Precision Medicines Nasdaq: PRAX · 5 drugs
- Precigen, Inc Nasdaq: PGEN · 3 drugs
- Prelude Therapeutics Incorporated Nasdaq: PRLD · 5 drugs
- Prime Medicine, Inc. Nasdaq: PRME · 3 drugs
- Prokidney Nasdaq: PROK · 1 drug
- ProMis Neurosciences, Inc Nasdaq: PMN · 1 drug
- ProQR Therapeutics Nasdaq: PRQR · 2 drugs
- Protagonist Therapeutics, Inc. Nasdaq: PTGX · 1 drug
- Protara Therapeutics Nasdaq: TARA · 2 drugs
- PTC Therapeutics Nasdaq: PTCT · 4 drugs
- Puma Biotechnology, Inc. Nasdaq: PBYI · 2 drugs
- Pyxis Oncology, Inc Nasdaq: PYXS · 3 drugs
- Q32 Bio Inc. Nasdaq: QTTB · 1 drug
- Quoin Pharmaceuticals Nasdaq: QNRX · 1 drug
- Radiopharm Theranostics, Ltd Nasdaq: RADX · 5 drugs
- Rapport Therapeutics Inc. Nasdaq: RAPP · 1 drug
- Recursion Pharmaceuticals Inc. Nasdaq: RXRX · 3 drugs
- Regeneron Pharmaceuticals Nasdaq: REGN · 77 drugs
- REGENXBIO Inc. Nasdaq: RGNX · 3 drugs
- Rein Therapeutics Nasdaq: RNTX · 1 drug
- Relay Therapeutics, Inc. Nasdaq: RLAY · 7 drugs
- Relmada Therapeutics, Inc. Nasdaq: RLMD · 2 drugs
- RenovoRx Nasdaq: RNXT · 1 drug
- Retension Pharmaceuticals. Inc. Nasdaq: RTSN · 1 drug
- Revolution Medicines, Inc. Nasdaq: RVMD · 19 drugs
- Rezolute Nasdaq: RZLT · 1 drug
- Rhythm Pharmaceuticals, Inc. Nasdaq: RYTM · 3 drugs
- Rigel Pharmaceuticals Nasdaq: RIGL · 3 drugs
- Rocket Pharmaceuticals Inc. Nasdaq: RCKT · 3 drugs
- SAb Biotherapeutics, Inc. Nasdaq: SABS · 1 drug
- Sagimet Biosciences Inc. Nasdaq: SGMT · 2 drugs
- Sana Biotechnology Nasdaq: SANA · 2 drugs
- Sanofi Nasdaq: SNY · 75 drugs
- Sarepta Therapeutics, Inc. Nasdaq: SRPT · 4 drugs
- Satellos Bioscience, Inc. Nasdaq: MSLE · 2 drugs
- Savara Inc. Nasdaq: SVRA · 1 drug
- Seaport Therapeutics Nasdaq: SPTX · 1 drug
- Sellas Life Sciences Group Nasdaq: SLS · 4 drugs
- Septerna, Inc. Nasdaq: SEPN · 1 drug
- Serina Therapeutics NYSE: SER · 1 drug
- Shattuck Labs, Inc. Nasdaq: STTK · 1 drug
- SIGA Technologies Nasdaq: SIGA · 1 drug
- Silence Therapeutics plc Nasdaq: SLN · 1 drug
- Skye Bioscience, Inc. Nasdaq: SKYE · 2 drugs
- Solid Biosciences Inc. Nasdaq: SLDB · 4 drugs
- Spruce Biosciences Nasdaq: SPRB · 1 drug
- Spyre Therapeutics, Inc. Nasdaq: SYRE · 5 drugs
- Stoke Therapeutics, Inc Nasdaq: STOK · 1 drug
- Summit Therapeutics Nasdaq: SMMT · 4 drugs
- Sutro Biopharma, Inc. Nasdaq: STRO · 3 drugs
- Syndax Pharmaceuticals Nasdaq: SNDX · 3 drugs
- Tango Therapeutics, Inc. Nasdaq: TNGX · 11 drugs
- Tarsus Pharmaceuticals, Inc. Nasdaq: TARS · 3 drugs
- Taysha Gene Therapies, Inc. Nasdaq: TSHA · 1 drug
- Tectonic Therapeutic Nasdaq: TECX · 1 drug
- Tempest Therapeutics Nasdaq: TPST · 3 drugs
- Tenax Therapeutics, Inc. Nasdaq: TENX · 1 drug
- Tenaya Therapeutics Nasdaq: TNYA · 2 drugs
- TG Therapeutics, Inc. Nasdaq: TGTX · 2 drugs
- Theriva Biologics SL NYSE: TOVX · 3 drugs
- Tiziana Life Sciences LTD Nasdaq: TLSA · 1 drug
- TransCode Therapeutics Nasdaq: RNAZ · 1 drug
- Travere Therapeutics, Inc. Nasdaq: TVTX · 2 drugs
- TRex Bio, Inc. Nasdaq: TRXB · 1 drug
- TriSalus Life Sciences, Inc. Nasdaq: TLSI · 1 drug
- TScan Therapeutics, Inc. Nasdaq: TCRX · 9 drugs
- TuHURA Biosciences, Inc. Nasdaq: HURA · 1 drug
- Turn Therapeutics Nasdaq: TTRX · 1 drug
- Tvardi Therapeutics, Incorporated Nasdaq: TVRD · 4 drugs
- Tyra Biosciences, Inc Nasdaq: TYRA · 4 drugs
- Ultragenyx Pharmaceutical Inc Nasdaq: RARE · 6 drugs
- United Therapeutics Nasdaq: UTHR · 2 drugs
- Upstream Bio Inc. Nasdaq: UPB · 1 drug
- UroGen Pharma Ltd. Nasdaq: URGN · 2 drugs
- Vanda Pharmaceuticals Nasdaq: VNDA · 9 drugs
- Vera Therapeutics, Inc. Nasdaq: VERA · 1 drug
- Veradermics, Inc. NYSE: MANE · 1 drug
- Verastem, Inc. Nasdaq: VSTM · 13 drugs
- Vericel Corporation Nasdaq: VCEL · 1 drug
- Verrica Pharmaceuticals Inc. Nasdaq: VRCA · 3 drugs
- Veru Inc. Nasdaq: VERU · 2 drugs
- Viatris Inc. Nasdaq: VTRS · 1 drug
- Viking Therapeutics, Inc. Nasdaq: VKTX · 1 drug
- Vir Biotechnology, Inc. Nasdaq: VIR · 6 drugs
- Vogenx, Inc. Nasdaq: VOGX · 1 drug
- Vor Biopharma Nasdaq: VOR · 1 drug
- Voyager Therapeutics Nasdaq: VYGR · 2 drugs
- vTv Therapeutics Nasdaq: VTVT · 1 drug
- Whitehawk Therapeutics, Inc. Nasdaq: WHWK · 3 drugs
- X4 Pharmaceuticals Nasdaq: XFOR · 1 drug
- XBiotech, Inc. Nasdaq: XBIT · 3 drugs
- Xencor, Inc. Nasdaq: XNCR · 7 drugs
- Xenon Pharmaceuticals Inc. Nasdaq: XENE · 1 drug
- Zura Bio Inc Nasdaq: ZURA · 1 drug
Sources: SEC EDGAR (exchange, ticker, filings and XBRL financial data, US Government works); ClinicalTrials.gov (U.S. National Library of Medicine), FDA (Drugs@FDA, Orange and Purple Book, orphan drugs) and EMA, data processed by Phuturdex and updated 13 November 2026. Active trials = recruiting or ongoing, phases I–III. The sponsor is the one stated by each trial; company names are linked to the SEC only when they are the same apart from the legal form. Patents, exclusivities, approvals and opinions are attributed to the company only when it holds them in the official register. No stock prices or charts. Only the official sources are authoritative.