Phuturdex › Diseases
Drugs in development · updated 30 October 2026
Drugs in development by disease
For 1,405 diseases, the drugs with active phase I–III clinical trials, updated 30 October 2026. Source: ClinicalTrials.gov.
Diseases with the most drugs in development
- Non-small-cell lung carcinoma 726
- Neoplasm 671
- Breast neoplasm 593
- Colorectal neoplasm 534
- Metastasis 493
- Ovarian neoplasm 411
- Pancreatic neoplasm 395
- Prostatic Neoplasms 383
- Melanoma 352
- Lung neoplasm 348
- Stomach neoplasm 340
- Triple-negative breast neoplasm 334
- Head and neck squamous cell carcinoma 321
- Acute myeloid leukemia 314
- Endometrial neoplasm 298
- Multiple myeloma 272
- Non-Hodgkin lymphoma 269
- Hepatocellular carcinoma 266
- Lymphoma 252
- Glioblastoma 245
- Obesity 233
- Renal cell carcinoma 228
- Uterine cervix neoplasm 224
- Hematologic neoplasm 216
All diseases (A–Z)
No disease found.
- Abdominal aortic aneurysm 3
- Abdominal pain 7
- Abortion, Habitual 3
- Abortion, Spontaneous 3
- Accelerated phase chronic myelogenous leukemia 28
- Achondroplasia 8
- Acidosis 3
- Acinar cell carcinoma 5
- Acne 16
- Acquired amegakaryocytic thrombocytopenia 6
- Acquired Immunodeficiency Syndrome 61
- Actinic keratosis 8
- Active peptic ulcer disease 3
- Acute abdomen 3
- Acute basophilic leukemia 3
- Acute biphenotypic leukaemia 80
- Acute chest syndrome 3
- Acute coronary syndrome 17
- Acute erythroid leukemia 3
- Acute kidney injury 37
- Acute liver failure 4
- Acute lung injury 9
- Acute megakaryoblastic leukemia 3
- Acute monocytic leukemia 22
- Acute myeloid leukemia 314
- Acute myelomonocytic leukemia 11
- Acute pain 20
- Acute promyelocytic leukemia 8
- Acute respiratory distress syndrome 43
- Acute-on-chronic liver failure 7
- Addictive behavior 4
- Adenocarcinoma 111
- Adenocarcinoma of the lung 50
- Adenocarcinoma, Follicular 13
- Adenoid cystic carcinoma 26
- Adenoma 4
- Adenomyosis 5
- Adenosquamous carcinoma 4
- Adenoviridae infections 13
- Adipose tissue neoplasm 4
- Adjustment disorder 3
- Adrenal cortex neoplasm 12
- Adrenal gland neoplasm 10
- Adrenocortical carcinoma 28
- Adrenoleukodystrophy 6
- Adult T-cell leukemia/lymphoma 10
- Adverse drug reaction 11
- Agammaglobulinemia 11
- Aggression 6
- Agnosia 19
- AIDS-related Kaposi sarcoma 3
- AIDS-related lymphoma 10
- Albuminuria 7
- Alcohol Drinking 11
- Alcohol-related disorders 3
- Alcoholic hepatitis 5
- Alcoholic liver cirrhosis 3
- Alcoholic liver disease 3
- Alcoholism 53
- Allergic bronchopulmonary aspergillosis 3
- Allergic conjunctivitis 6
- Allergic contact dermatitis 10
- Allergic rhinitis 5
- Alopecia 31
- Alopecia areata 22
- Alopecia universalis 3
- Alpha-1-antitrypsin deficiency 11
- Alpha-mannosidosis 6
- Alveolar rhabdomyosarcoma 7
- Alveolar soft part sarcoma 29
- Alzheimer's disease 157
- Amyloid 9
- Amyloidosis 24
- Amyloidosis, Familial 3
- Amyloidosis, Hereditary, Transthyretin-Related 3
- Amyotrophic lateral sclerosis 79
- Anal Canal Carcinoma 8
- Anaphylaxis 16
- Anaplastic large-cell lymphoma 36
- Anaplastic thyroid carcinoma 24
- Anemia 52
- Aneurysm 4
- Angelman syndrome 4
- Angina pectoris 5
- Angiomatoid fibrous histiocytoma 4
- Anhedonia 5
- Ankylosing spondylitis 31
- Anophthalmia with pulmonary hypoplasia 11
- Anorexia 11
- Anorexia nervosa 8
- Anovulation 3
- Anterior cruciate ligament injury 5
- Anti-N-Methyl-D-Aspartate Receptor Encephalitis 4
- Anti-neutrophil cytoplasmic antibody-associated vasculitis 35
- Antiphospholipid syndrome 6
- Anus neoplasm 28
- Anxiety disorder 32
- Aortic valve calcification 3
- Aortic valve disease 4
- Aortic valve stenosis 13
- Aplastic anemia 43
- Apnea 4
- Appendiceal neoplasm 28
- Appendicitis 7
- Arbovirus Infections 3
- Arrhythmias, Cardiac 10
- Arrhythmogenic right ventricular cardiomyopathy 5
- Arterial hypertension 119
- Arterial pulmonary hypertension 27
- Arteriovenous malformation 5
- Arthralgia 5
- Arthritis 13
- Arthritis, Juvenile 39
- Ascending cholangitis 3
- Ascites 4
- Aspergillosis 3
- Asphyxia neonatorum 5
- Asthma 84
- Astrocytoma 64
- Ataxia 6
- Ataxia telangiectasia 3
- Atherosclerosis 34
- Atopic dermatitis 91
- Atrial fibrillation 32
- Atrial flutter 6
- Atrophic muscular disease 3
- Atrophy 7
- Attention deficit hyperactivity disorder 14
- Atypical chronic myeloid leukemia 22
- Atypical hemolytic uremic syndrome 5
- Autism spectrum disorder 35
- Autistic Disorder 22
- Autoimmune disease 94
- Autoimmune disease of the nervous system 21
- Autoimmune hemolytic anemia 13
- Autoimmune hepatitis 6
- Autoimmune lymphoproliferative syndrome 6
- Autoimmune thrombocytopenic purpura 53
- Autonomic nervous system disease 5
- Autosomal dominant Parkinson disease 4 7
- Autosomal dominant polycystic kidney 30
- Autosomal recessive limb-girdle muscular dystrophy type 2I 3
- Axial spondyloarthritis 5
- B-cell leukemia 49
- B-cell lymphoma 152
- B-cell prolymphocytic leukemia 7
- Back Injuries 3
- Back pain 8
- Bacteremia 8
- Bacterial Infections 16
- Bacterial meningitis 5
- Bacterial pneumonia 4
- Bacterial vaginosis 17
- Bacteriuria 3
- Barrett's esophagus 5
- Basal-cell carcinoma of the skin 28
- Basal-cell neoplasm 3
- Behcet Syndrome 11
- Beta thalassemia 34
- Bietti crystalline corneoretinal dystrophy 3
- Bile duct neoplasm 36
- Biliary atresia 5
- Biliary tract neoplasm 139
- Binge eating disorder 4
- Bipolar disorder 29
- Bites and stings 15
- Bladder disease 9
- Bladder neoplasm 185
- Blast Crisis 32
- Blastic plasmacytoid dendritic cell neoplasm 24
- Blindness 6
- Blood coagulation disease 4
- Blood protein disease 9
- Bone disease 9
- Bone marrow disease 14
- Bone marrow failure 26
- Bone marrow neoplasm 3
- Bone neoplasm 25
- Bone resorption 3
- Borderline personality disorder 6
- Bradycardia 4
- Brain Diseases 23
- Brain hypoxia-ischemia 14
- Brain infarction 3
- Brain Injuries 11
- Brain Neoplasms 190
- Brain stem infarction 3
- Breakthrough pain 3
- Breast carcinoma in situ 11
- Breast disease 21
- Breast ductal carcinoma 10
- Breast Feeding 10
- Breast lobular carcinoma 16
- Breast neoplasm 593
- Brenner tumor 6
- Bronchial disease 4
- Bronchial neoplasm 17
- Bronchiectasis 8
- Bronchiolitis obliterans 6
- Bronchiolitis obliterans syndrome 36
- Bronchiolo-alveolar adenocarcinoma 11
- Bronchitis 6
- Bronchopulmonary dysplasia 11
- Bulbo-Spinal Atrophy, X-Linked 8
- Bunion 3
- Burkitt lymphoma 113
- Burn 11
- Bursitis 3
- Cachexia 9
- Calciphylaxis 4
- Camurati-Engelmann disease 5
- Cancer pain 11
- Candidemia 3
- Capsular contracture 3
- Carcinoid tumor 15
- Carcinoma 137
- Carcinoma, Bronchogenic 16
- Carcinoma, Endometrioid 13
- Carcinosarcoma 25
- Cardio-Renal Syndrome 3
- Cardiogenic shock 13
- Cardiomegaly 3
- Cardiomyopathies 23
- Cardiotoxicity 21
- Cardiovascular disease 71
- Carotid artery disease 3
- Carotid artery stenosis 4
- Carpal tunnel syndrome 3
- Castleman's disease 3
- Castration-resistant prostatic neoplasm 44
- Cataplexy 4
- Cataract 10
- Catecholaminergic polymorphic ventricular tachycardia 3
- Celiac disease 7
- Central nervous system disease 38
- Central nervous system neoplasm 70
- Central nervous system trauma 4
- Central nervous system vasculitis 6
- Central sleep apnea 3
- Cerebral amyloid angiopathy 4
- Cerebral hemorrhage 23
- Cerebral infarction 7
- Cerebral palsy 8
- Cerebral small vessel diseases 5
- Cerebrovascular disease 8
- Charcot–Marie–Tooth disease 3
- Chediak-Higashi syndrome 5
- Chickenpox 13
- Cholangiocarcinoma 136
- Cholera 3
- Cholestasis 6
- Chondrocalcinosis 5
- Chondrosarcoma 13
- Chordoma 11
- Chorea 3
- Choriocarcinoma 9
- Choroidal neovascularization 5
- Chromosome 17 deletion 4
- Chromosome 7, monosomy 8
- Chromosome Aberrations 8
- Chronic arterial occlusive disease 3
- Chronic bronchitis 3
- Chronic cough 9
- Chronic eosinophilic leukemia 10
- Chronic granulomatous disease 21
- Chronic hepatitis 4
- Chronic hepatitis B 42
- Chronic hepatitis D 7
- Chronic inducible urticaria 6
- Chronic inflammatory demyelinating polyradiculoneuropathy 23
- Chronic kidney disease-mineral and bone disorder 4
- Chronic kidney failure 48
- Chronic Limb-Threatening Ischemia 5
- Chronic lymphocytic leukemia 137
- Chronic myelomonocytic leukemia 90
- Chronic neutrophilic leukemia 14
- Chronic obstructive pulmonary disease 89
- Chronic pain 40
- Chronic pancreatitis 8
- Chronic phase chronic myelogenous leukemia 35
- Chronic progressive multiple sclerosis 39
- Chronic renal insufficiency 104
- Chronic subdural hematoma 4
- Chronic urticaria 24
- Churg-Strauss syndrome 7
- Cicatrix 4
- Cigarette smoking 7
- Circadian rhythm sleep disorder 4
- Circulating tumor cell 9
- Clear cell adenocarcinoma 17
- Clear-cell metastatic renal cell carcinoma 26
- Clear-cell sarcoma 14
- Clostridium Infections 13
- Cluster headache 7
- Cocaine-related disorder 3
- Cognition Disorders 6
- Cognitive dysfunction 94
- Cold urticaria 4
- Colitis 24
- Colonic disease 11
- Colonic neoplasm 157
- Colorectal Cancer, Hereditary Nonpolyposis, Type 6 3
- Colorectal neoplasm 534
- Colorectal Neoplasms, Hereditary Nonpolyposis 12
- Combat disorder 4
- Common cold 4
- Common variable immunodeficiency 14
- Communicable Diseases 12
- Community-acquired pneumonia 45
- Complications of pregnancy 3
- Concussion 10
- Cone-rod dystrophy 5
- Congenital Abnormalities 14
- Congenital adrenal hyperplasia 7
- Congenital amegakaryocytic thrombocytopenia 5
- Congenital bone marrow failure syndromes 8
- Congenital fibrosis of the extraocular muscles 5
- Congenital heart disease 8
- Congenital hemolytic anemia 4
- Congenital hyperinsulinism 4
- Congenital structural myopathy 4
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities 4
- Connective tissue disease 21
- Constipation 12
- Corneal disease 6
- Corneal edema 3
- Coronary artery disease 34
- Coronary Disease 3
- Coronavirus disease 18
- Cough 14
- COVID-19 104
- Cranial nerve disease 4
- Craniopharyngioma 19
- Critical illness 19
- Crohn's disease 81
- Cryptosporidiosis 3
- Cushing's syndrome 9
- Cutaneous leishmaniasis 11
- Cutaneous lupus erythematosus 17
- Cutaneous malignant melanoma 13
- Cutaneous T cell lymphoma 46
- Cutis laxa 3
- Cystic fibrosis 30
- Cysticercosis 3
- Cystinosis 6
- Cytokine release syndrome 21
- Cytomegalovirus Infections 6
- Cytopenia 14
- Deafness 3
- Death 3
- Degenerative myopia 4
- Deglutition Disorders 4
- Delayed graft function 4
- Delirium 14
- Dementia 54
- Demyelinating disease 6
- Dengue fever 15
- Dental plaque 3
- Dental pulp disease 5
- Dental pulp necrosis 3
- Dentin Sensitivity 3
- Depression 73
- Depressive disorder 12
- Depressive Disorder, Treatment-Resistant 21
- Dermatitis 29
- Dermatitis, Seborrheic 3
- Dermatofibrosarcoma protuberans 13
- Dermatomyositis 52
- Desmoid Tumors 11
- Desmoplastic small-round-cell tumor 19
- Diabetes 91
- Diabetes insipidus 8
- Diabetic foot 6
- Diabetic ketoacidosis 4
- Diabetic Nephropathies 18
- Diabetic Neuropathies 12
- Diabetic retinopathy 17
- Diamond-Blackfan anemia 8
- Diarrhea 12
- Diffuse Intrinsic Pontine Glioma 40
- Diffuse large B-cell lymphoma 177
- Diffuse scleroderma 39
- Digestive System Diseases 36
- Digestive system neoplasm 37
- Dihydropyrimidine dehydrogenase deficiency 6
- Dilatation, Pathologic 3
- Dilated cardiomyopathy 7
- Discoid lupus erythematosus 8
- Disorder of consciousness 3
- Disorder of sex development 4
- Disorders of Excessive Somnolence 10
- Dizziness 6
- DNA repair-deficiency disorder 4
- DNA virus infectious disease 6
- Down syndrome 36
- Drug Hypersensitivity 17
- Drug Hypersensitivity Syndrome 4
- Drug Resistant Epilepsy 9
- Dry eye syndrome 18
- Dry Socket 3
- Duchenne muscular dystrophy 35
- Duodenal neoplasm 4
- Dust mite allergy 3
- Dwarfism 3
- Dwarfism, Pituitary 6
- Dyskeratosis congenita 15
- Dyskinesia 3
- Dyslipidemia 35
- Dysmenorrhea 3
- Dyspareunia 3
- Dyspepsia 9
- Dyspnea 7
- Dystonia 3
- Ear disease 4
- Eating disorder 5
- Eczema 27
- Eczematous skin disease 3
- Edema 9
- Embryonal carcinoma 9
- Embryonal rhabdomyosarcoma 6
- Emergence delirium 18
- Emerging communicable disease 4
- Emphysema 13
- Encephalitis 5
- End-stage liver disease 4
- Endocrine gland neoplasm 3
- Endocrine system disease 19
- Endodermal sinus tumor 7
- Endometrial hyperplasia 14
- Endometrial neoplasm 298
- Endometrial stromal sarcoma 3
- Endometriosis 16
- Enterocolitis, Pseudomembranous 3
- Enteropathy-associated T-cell lymphoma 13
- Eosinophilic esophagitis 8
- Ependymoma 56
- Epidermolysis bullosa 6
- Epidermolysis bullosa dystrophica 8
- Epidermolysis bullosa simplex 3
- Epilepsies, Myoclonic 7
- Epilepsies, Partial 7
- Epilepsy 44
- Epistaxis 6
- Epithelioid hemangioendothelioma 6
- Epstein–Barr virus infection 30
- Erdheim-Chester disease 6
- Erectile dysfunction 32
- Erythema 6
- Escherichia coli infectious disease 4
- Esophageal disease 5
- Esophageal neoplasm 191
- Esophageal squamous cell carcinoma 115
- Esophagus adenocarcinoma 82
- Essential hypertension 31
- Esthesioneuroblastoma 10
- Eunuchism 3
- Evans' syndrome 3
- Ewing sarcoma 82
- Exanthema 6
- Exocrine pancreatic insufficiency 6
- Exophthalmos 5
- Experimental neoplasm 4
- Extramammary Paget's disease 13
- Extranodal NK/T-cell lymphoma, nasal type 35
- Extraskeletal myxoid chondrosarcoma 4
- Extrinsic allergic alveolitis 3
- Eye disease 19
- Eye neoplasm 4
- Fabry disease 10
- Facial pain 5
- Facioscapulohumeral muscular dystrophy 7
- Fallopian tube disease 3
- Fallopian tube neoplasm 124
- Familial adenomatous polyposis 9
- Familial amyloid neuropathy 4
- Familial dermographism 4
- Familial ependymoma 4
- Familial hyperchylomicronemia syndrome 3
- Fanconi anemia 16
- Fatigue 24
- Fatty liver disease 23
- Febrile neutropenia 6
- Fecal incontinence 5
- Female infertility 11
- Female urogenital disease 11
- Female urogenital diseases and pregnancy complications 3
- Fetal Growth Retardation 5
- Fever 4
- Fibrolamellar hepatocellular carcinoma 22
- Fibromyalgia 6
- Fibrosarcoma 8
- Fibrosis 52
- Filarial elephantiasis 3
- Flavivirus Infections 3
- Focal cortical dysplasia 3
- Focal segmental glomerulosclerosis 15
- Follicular lymphoma 144
- Food Hypersensitivity 7
- Fractures, Bone 8
- Fragile X syndrome 10
- Frailty syndrome 15
- Friedreich ataxia 9
- Frontotemporal dementia 11
- Fuchs' endothelial dystrophy 4
- Gallbladder neoplasm 55
- Ganglioneuroblastoma 20
- Gangliosidoses 4
- Gastritis 6
- Gastro-enteropancreatic neuroendocrine tumor 22
- Gastroenteritis 4
- Gastroesophageal reflux disease 9
- Gastrointestinal disease 22
- Gastrointestinal Hemorrhage 6
- Gastrointestinal neoplasm 80
- Gastrointestinal stromal tumor 36
- GATA2 deficiency 18
- Gaucher's disease 18
- Gender dysphoria 4
- Generalized anxiety disorder 12
- Genetic disease 33
- Genetic predisposition to disease 5
- Genital Diseases 7
- Genital Diseases, Female 6
- Genital Diseases, Male 8
- Genital Neoplasms, Female 14
- Genital Neoplasms, Male 6
- Geographic atrophy 26
- Germ cell and embryonal neoplasms 35
- Germinoma 7
- Gestational diabetes 9
- Gestational trophoblastic disease 9
- Giant cell arteritis 30
- Giant-cell tumor of bone 8
- Giant-cell tumor of the tendon sheath 3
- Gingivitis 5
- Glandular and epithelial neoplasm 12
- Glaucoma 14
- Glioblastoma 245
- Glioma 184
- Gliosarcoma 34
- Glomerulonephritis 13
- Glomus tumor 4
- Glucose intolerance 6
- Glucose metabolism disease 12
- Glycogen storage disease 4
- Glycogen storage disease II 9
- Gonadal disease 3
- Gonorrhea 8
- Gout 13
- Gouty arthritis 5
- Graft-versus-host disease 49
- Gram-negative bacterial infection 3
- Granular cell tumor 4
- Granulomatosis with polyangiitis 36
- Graves' disease 13
- Graves' ophthalmopathy 19
- Growth disorder 4
- Guillain–Barré syndrome 3
- Gulf War syndrome 4
- Hair diseases 3
- Hairy cell leukemia 32
- Hallucination 5
- Hashimoto Disease 3
- Head and neck neoplasms 184
- Head and neck squamous cell carcinoma 321
- Headache 12
- Healthcare-associated pneumonia 3
- Hearing Loss 13
- Heart Arrest 13
- Heart disease 17
- Heart failure 104
- Heart Failure, Diastolic 4
- Heart valve disease 3
- Helicobacter infection 5
- Hemangiosarcoma 58
- Hematologic Diseases 57
- Hematologic neoplasm 216
- Hemoglobinopathies 22
- Hemolysis 3
- Hemolytic anemia 6
- Hemophagocytic lymphohistiocytosis 13
- Hemophilia A 26
- Hemophilia B 10
- Hemorrhage 25
- Hemorrhagic disease 6
- Hemorrhagic shock 3
- Hemorrhagic stroke 3
- Hemostatic Disorders 6
- Hepatic encephalopathy 7
- Hepatic insufficiency 11
- Hepatitis 11
- Hepatitis B 28
- Hepatitis C 6
- Hepatitis D 5
- Hepatoblastoma 41
- Hepatocellular carcinoma 266
- Hepatolenticular Degeneration 7
- Hereditary angioedema 8
- Hereditary diffuse leukoencephalopathy with spheroids 5
- Hereditary eye disease 4
- Hereditary hemorrhagic telangiectasia 8
- Hereditary leiomyomatosis and renal cell cancer syndrome 5
- Hereditary sensory and autonomic neuropathy 6
- Herpes simplex 3
- Herpes zoster 7
- Heterotopic ossification 3
- Hidden hearing loss 4
- Hidradenitis 9
- Hidradenitis suppurativa 36
- Hip Fractures 7
- Hip osteoarthritis 4
- Histiocytic sarcoma 15
- Histiocytoma, Malignant Fibrous 19
- Histiocytosis 9
- Histiocytosis, Sinus 5
- HIV infection 84
- HIV seropositivity 4
- Hodgkin lymphoma 93
- Homozygous familial hypercholesterolemia 7
- Hookworm disease 4
- Hot flash 8
- Hoyeraal-Hreidarsson syndrome 9
- HTLV-I Infections 7
- Human body weight 13
- Huntington's disease 14
- Hyperaldosteronism 7
- Hyperalgesia 3
- Hypercalcemia 3
- Hypercholesterolemia 21
- Hypereosinophilic syndrome 8
- Hyperglycemia 8
- Hyperinsulinism 14
- Hyperkalemia 3
- Hyperlipidemia 26
- Hyperlipoproteinemia 3
- Hyperlipoproteinemia Type II 12
- Hyperphagia 3
- Hyperphosphatemia 4
- Hypersensitivity 22
- Hypertension, Pregnancy-Induced 7
- Hyperthermia 6
- Hyperthyroidism 8
- Hypertriglyceridemia 18
- Hypertrophic cardiomyopathy 16
- Hyperuricemia 13
- Hypoglycemia 20
- Hypogonadism 8
- Hypoparathyroidism 3
- Hypopharyngeal Neoplasms 33
- Hypotension 11
- Hypothyroidism 4
- Hypoxia 20
- Idiopathic hypersomnia 7
- Idiopathic interstitial pneumonia 4
- Idiopathic pulmonary fibrosis 57
- IgA glomerulonephritis 48
- IgA Vasculitis 5
- Immune Deficiency Disease 6
- Immune dysregulation-polyendocrinopathy-enteropathy-X-linked syndrome 6
- Immune System Diseases 54
- Immunoblastic lymphadenopathy 32
- Immunoglobulin G4-Related Disease 14
- Immunoglobulin Light-chain Amyloidosis 27
- Immunologic Deficiency Syndromes 17
- Immunoproliferative disorder 16
- Impulse control disorder 6
- In situ carcinoma 10
- Inborn metabolic brain disease 3
- Inclusion body myositis 3
- Infection 71
- Infection of the central nervous system 6
- Infectious mononucleosis 5
- Infertility 24
- Inflammation 85
- Inflammatory bowel diseases 69
- Inflammatory breast cancer 18
- Influenza 68
- Infratentorial neoplasm 8
- Inguinal hernia 4
- Insulin resistance 41
- Intellectual disability 7
- Interdigitating dendritic cell sarcoma 30
- Intermittent claudication 7
- Interstitial cystitis 10
- Interstitial lung disease 65
- Intervertebral Disc Degeneration 3
- Intestinal disease 15
- Intestinal failure 3
- Intestinal neoplasm 16
- Intraabdominal infection 5
- Intracranial arteriosclerosis 8
- Intracranial Hemorrhages 5
- Intracranial thrombosis 4
- Intraductal carcinoma of the breast 18
- Intraocular lymphoma 3
- Invasive candidiasis 3
- Iron Deficiencies 11
- Iron deficiency anemia 7
- Iron overload 4
- Irritable bowel syndrome 17
- Ischemia 5
- Ischemic Attack, Transient 5
- Ischemic stroke 94
- Islet cell adenoma 18
- Job's syndrome 4
- Joint Diseases 6
- Junctional epidermolysis bullosa 3
- Juvenile myelomonocytic leukemia 28
- Juvenile xanthogranuloma 15
- Kaposi's sarcoma 15
- Keratoconus 3
- Ketosis 6
- Kidney Calculi 11
- Kidney disease 38
- Kidney neoplasm 92
- Klatskin's tumor 17
- Klinefelter's syndrome 4
- Knee Injuries 3
- Knee osteoarthritis 37
- Laceration 3
- Lacunar stroke 4
- Lambert-Eaton myasthenic syndrome 6
- Langerhans-cell histiocytosis 37
- Language disorder 3
- Large cell carcinoma 5
- Large-cell immunoblastic lymphoma 10
- Laryngeal disease 14
- Laryngeal neoplasm 35
- Lassa fever 4
- Latent tuberculosis 6
- Leber congenital amaurosis 10
- Leber hereditary optic neuropathy 4
- Lecithin Cholesterol Acyltransferase Deficiency 4
- Left ventricular dysfunction 10
- Left ventricular hypertrophy 4
- Leg Injuries 6
- Leiomyoma 9
- Leiomyosarcoma 36
- Leishmaniasis 3
- Lennox-Gastaut sindrome 4
- Leprosy 3
- Leukemia 153
- Leukemia, Large Granular Lymphocytic 24
- Leukemia, Myelogenous, Chronic, BCR-ABL Positive 68
- Leukocyte adhesion deficiency type 1 6
- Leukodystrophy, Globoid Cell 8
- Leukopenia 3
- Lewy body dementia 7
- Lichen planus 5
- Limb-girdle muscular dystrophy 3
- Lip neoplasm 6
- Lipid metabolism disorder 4
- Lipidoses 3
- Lipoid nephrosis 13
- Liposarcoma 43
- Liver abscess 3
- Liver cirrhosis 38
- Liver Cirrhosis, Biliary 13
- Liver disease 33
- Liver failure 10
- Liver neoplasm 86
- Local neoplasm recurrence 12
- Lower back pain 12
- Lower urinary tract symptoms 4
- Lung disease 104
- Lung neoplasm 348
- Lung small cell carcinoma 197
- Lupus nephritis 64
- Lyme disease 3
- Lymphadenopathy 13
- Lymphangioma 3
- Lymphatic Abnormalities 7
- Lymphatic metastasis 13
- Lymphatic system disease 20
- Lymphedema 7
- Lymphoid leukemia 18
- Lymphoma 252
- Lymphoma, B-Cell, Marginal Zone 86
- Lymphomatoid papulosis 3
- Lymphopenia 3
- Lymphoproliferative disorders 51
- Lysosomal storage disease 11
- Macular degeneration 40
- Macular retinal edema 15
- Major depressive disorder 72
- Malaria 21
- Male breast neoplasm 18
- Male infertility 7
- Male urogenital disease 19
- Malignant mesenchymal tumor 9
- Malignant mesothelioma 58
- Malignant ovarian germ cell neoplasm 5
- Malignant pleural effusion 7
- Mania 6
- Mantle cell lymphoma 108
- Marijuana Abuse 22
- Mast cell leukemia 7
- Mediastinal neoplasm 9
- Medication adherence 7
- Medullary carcinoma 13
- Medulloblastoma 77
- Melanoma 352
- Melanosis 4
- MELAS syndrome 3
- Membranoproliferative glomerulonephritis 7
- Membranous glomerulonephritis 13
- Memory disorder 7
- Meniere's disease 3
- Meningeal carcinomatosis 28
- Meningeal neoplasm 14
- Meningioma 33
- Meningitis 5
- Meningococcal disease 4
- Menorrhagia 4
- Mental disorder 24
- Mental fatigue 4
- Merkel cell carcinoma 48
- Mesothelioma 54
- Metabolic bone disease 4
- Metabolic brain disease 3
- Metabolic disease 30
- Metabolic syndrome 12
- Metabolism, Inborn Errors 6
- Metachromatic leukodystrophy 7
- Metastasis 493
- Metrorrhagia 4
- Microsatellite instability 21
- Microscopic polyangiitis 6
- Microvascular angina 7
- Migraine 28
- Migraine with aura 4
- Migraine without aura 4
- Mitochondrial disease 10
- Monoclonal gammopathy of uncertain significance 3
- Mood disorder 8
- Morbid obesity 3
- Mosquito-borne disease 3
- Motor activity 4
- Motor neuron disease 10
- Mouth Neoplasms 49
- Movement disorders 13
- Mpox 5
- Mucinous adenocarcinoma 14
- Mucocutaneous Lymph Node Syndrome 5
- Mucopolysaccharidoses 5
- Mucopolysaccharidosis I 7
- Mucopolysaccharidosis II 15
- Mucopolysaccharidosis III 8
- Mucopolysaccharidosis IV 3
- Mucopolysaccharidosis VI 3
- Mucositis 5
- Multi-centric Castleman's Disease 15
- Multidrug-resistant tuberculosis 12
- Multiple endocrine neoplasia type 1 4
- Multiple myeloma 272
- Multiple sclerosis 93
- Multiple system atrophy 19
- Muscle weakness 4
- Muscular atrophy 5
- Muscular disease 12
- Muscular Dystrophies 9
- Musculoskeletal disorder 22
- Musculoskeletal pain 3
- Myalgic encephalomyelitis/chronic fatigue syndrome 7
- Myasthenia gravis 49
- Mycobacterium Infections 8
- Mycobacterium Infections, Nontuberculous 27
- Mycoses 5
- Mycosis fungoides 40
- Myelin Oligodendrocyte Glycoprotein Antibody-Associated Disease 9
- Myelodysplastic Syndromes 203
- Myelodysplastic–myeloproliferative diseases 40
- Myelofibrosis 91
- Myeloid leukemia 26
- Myeloid sarcoma 21
- Myeloproliferative disorders 91
- Myocardial infarction 26
- Myocardial infarction with ST segment elevation 22
- Myocardial ischemia 6
- Myocardial reperfusion injury 3
- Myocarditis 8
- Myoepithelioma 5
- Myopia 5
- Myositis 42
- Myositis ossificans 4
- Myotonia 3
- Myotonic dystrophy 10
- Myxoid liposarcoma 15
- Narcolepsy 10
- Nasal Obstruction 8
- Nasopharyngeal Carcinoma 71
- Nasopharyngeal disease 3
- Nasopharyngeal neoplasm 32
- Nausea 15
- Necrosis 9
- Neonatal alloimmune thrombocytopenia 3
- Neonatal sepsis 3
- Neoplasm 671
- Neoplasms, Unknown Primary 10
- Neoplastic Processes 7
- Nephritis 7
- Nephritis, Hereditary 5
- Nephrocalcinosis 4
- Nephrolithiasis 14
- Nephrotic syndrome 15
- Nerve sheath neoplasms 7
- Nerve tissue neoplasm 4
- Nervous System Diseases 39
- Nervous system heredodegenerative disease 3
- Nervous system neoplasm 4
- Neuralgia 21
- Neurobehavioral manifestation 8
- Neuroblastoma 95
- Neurocognitive Disorders 10
- Neurocysticercosis 3
- Neurodegenerative Diseases 25
- Neurodevelopmental disorder 14
- Neuroectodermal tumor 3
- Neuroendocrine carcinoma 55
- Neuroendocrine tumor 84
- Neuroepithelial neoplasm 4
- Neurofibroma 4
- Neurofibromatoses 4
- Neurofibromatosis 1 28
- Neurofibromatosis 2 10
- Neurofibrosarcoma 24
- Neurogenic bladder 4
- Neuroinflammatory diseases 15
- Neurologic Manifestations 15
- Neuroma, Acoustic 9
- Neuromuscular disease 14
- Neuromuscular manifestations 5
- Neuromyelitis optica 25
- Neuronal ceroid lipofuscinosis 5
- Neurotoxicity Syndromes 12
- Neutropenia 12
- Niemann–Pick disease, type C 3
- No reflow phenomenon 3
- Nocturia 5
- Nocturnal enuresis 3
- Non-alcoholic Fatty Liver Disease 68
- Non-Hodgkin lymphoma 269
- Non-muscle invasive bladder neoplasm 50
- Non-small-cell lung carcinoma 726
- Non-ST elevated myocardial infarction 3
- Nonseminomatous germ cell tumor 7
- Noonan syndrome 4
- Nutrition disorder 10
- Nutritional and metabolic diseases 5
- Obesity 233
- Obsessive-compulsive disorder 17
- Obstetric labor complication 4
- Obstructive lung disease 4
- Obstructive sleep apnea 32
- Ocular hypertension 9
- Ocular onchocerciasis 4
- Oligodendroglioma 26
- Oligospermia 3
- Onchocerciasis 4
- Onychomycosis 3
- Open-angle glaucoma 12
- Opioid-related disorders 49
- Opportunistic infection 11
- Opsoclonus myoclonus syndrome 6
- Optic nerve disease 6
- Optic nerve glioma 6
- Optic neuritis 6
- Oral lichen planus 6
- Oral mucosa leukoplakia 3
- Ornithine carbamoyltransferase deficiency 6
- Oropharyngeal Neoplasms 46
- Orthostatic hypotension 3
- Orthostatic intolerance 6
- Osteoarthritis 20
- Osteochondrodysplasia 3
- Osteogenesis imperfecta 4
- Osteomyelitis 4
- Osteonecrosis 5
- Osteopetrosis 7
- Osteoporosis 10
- Osteosarcoma 101
- Otorhinolaryngologic disease 4
- Ototoxicity 3
- Out-of-hospital cardiac arrest 6
- Ovarian disease 10
- Ovarian epithelial carcinoma 66
- Ovarian granulosa cell tumor 3
- Ovarian neoplasm 411
- Overactive bladder 9
- Overnutrition 5
- Overweight 139
- Oxyphilic adenoma 3
- Pachyonychia congenita 3
- Pain 75
- Pancoast Syndrome 5
- Pancreatic cancer, adult 11
- Pancreatic Diseases 8
- Pancreatic ductal carcinoma 23
- Pancreatic neoplasm 395
- Pancreatitis 15
- Papillary renal cell carcinomas 4
- Papillary thyroid cancer 15
- Papilloma 3
- Papillomavirus infections 16
- Paraganglioma 24
- Paramyxoviridae Infections 4
- Paranasal sinus disease 3
- Paranasal sinus neoplasm 7
- Paraneoplastic Syndromes 3
- Paraproteinemia 13
- Parasomnia 4
- Parathyroid neoplasm 4
- Parkinson's disease 104
- Parkinsonian Disorders 6
- Paroxysmal nocturnal hemoglobinuria 36
- Patent ductus arteriosus 3
- Patent foramen ovale 6
- Patient compliance 3
- Patient preference 7
- Peanut Hypersensitivity 11
- Pediatric Obesity 11
- Pelvic pain 7
- Pemphigus 9
- Penile neoplasm 26
- Peptic ulcer disease 5
- Perennial allergic rhinitis 3
- Periapical periodontitis 5
- Pericarditis 6
- Periodontal disease 3
- Periodontitis 9
- Peripheral Arterial Disease 25
- Peripheral nerve injury 5
- Peripheral Nervous System Diseases 16
- Peripheral primitive neuroectodermal tumor 17
- Peripheral T-cell lymphoma 71
- Peripheral vascular disease 7
- Peritoneal neoplasm 30
- Perivascular epithelioid cell neoplasm 5
- Pharyngeal Neoplasms 5
- Pharyngitis 5
- Phenylketonuria 16
- Pheochromocytoma 29
- Philadelphia chromosome 13
- Phlebitis 3
- Phobia, Social 3
- Pick disease 8
- Pigmented villonodular synovitis 3
- Pinealoma 21
- Plaque, Atherosclerotic 5
- Plasma cell leukemia 22
- Plasma cell neoplasm 45
- Plasmablastic lymphoma 19
- Plasmacytoma 4
- Plasmodium falciparum malaria 21
- Plasmodium vivax malaria 9
- Platelet Glycoprotein IV Deficiency 3
- Pleuropulmonary blastoma 7
- Plexiform neurofibroma 12
- Pneumococcal infection 8
- Pneumonia 63
- Pneumonia, Pneumocystis 4
- POEMS syndrome 5
- Polycystic Ovary Syndrome 11
- Polycythemia 5
- Polycythemia vera 49
- Polymyalgia rheumatica 30
- Polymyositis 36
- Polyneuropathies 3
- Portal hypertension 8
- Post-Acute COVID-19 Syndrome 44
- Post-dural-puncture headache 4
- Post-traumatic stress disorder 39
- Postherpetic neuralgia 3
- Postmenopausal osteoporosis 6
- Postoperative cognitive dysfunction 5
- Postoperative complications 4
- Postoperative hemorrhage 3
- Postoperative nausea and vomiting 8
- Postoperative pain 50
- Postoperative wounds infection 7
- Postpartum depression 9
- Postpartum hemorrhage 4
- Postthrombotic Syndrome 3
- Postural orthostatic tachycardia syndrome 20
- Pouchitis 3
- Prader–Willi syndrome 5
- Pre-eclampsia 23
- Precancerous Conditions 12
- Precursor B-cell lymphoblastic leukemia 31
- Precursor lymphoblastic lymphoma/leukemia 163
- Precursor T-cell lymphoblastic leukemia 61
- Prediabetes 18
- Preleukemia 10
- Premature Birth 31
- Preterm premature rupture of the membranes 3
- Primary Dysautonomias 4
- Primary effusion lymphoma 13
- Primary hyperoxaluria 4
- Primary hyperoxaluria type I 4
- Primary immunodeficiency disease 13
- Primary Ovarian Insufficiency 8
- Primary pulmonary hypertension 11
- Primitive neuroectodermal tumor 31
- Progressive supranuclear palsy 7
- Prolymphocytic leukemia 15
- Prostatic Diseases 8
- Prostatic Hyperplasia 16
- Prostatic Neoplasms 383
- Proteinuria 19
- Proteostasis Deficiencies 7
- Pruritus 18
- Pseudomonas infection 3
- Pseudomyxoma peritonei 12
- Psoriasis 46
- Psoriatic arthritis 48
- Psychomotor agitation 10
- Psychotic disorder 23
- Pulmonary embolism 11
- Pulmonary Eosinophilia 3
- Pulmonary fibrosis 34
- Pulmonary hypertension 38
- Pulmonary sarcoidosis 6
- Pulmonary tuberculosis 36
- Pure autonomic failure 3
- Pyoderma gangrenosum 7
- Pyruvate Dehydrogenase Complex Deficiency Disease 3
- Quadriplegia 4
- Radiation Injuries 13
- Radiation Pneumonitis 5
- Rare disease 12
- Rasmussen's encephalitis 6
- Rectal disease 9
- Rectal neoplasm 131
- Recurrent respiratory papillomatosis 5
- Red meat allergy 3
- Refractory anemia with excess of blasts 35
- Relapsing polychondritis 7
- Relapsing-remitting multiple sclerosis 26
- REM sleep behavior disorder 6
- Renal cell carcinoma 228
- Renal colic 4
- Renal Insufficiency 51
- Reperfusion injury 8
- Residual neoplasm 98
- Respiration disorder 6
- Respiratory disease 57
- Respiratory Insufficiency 25
- Respiratory sound 4
- Respiratory syncytial virus infectious disease 12
- Respiratory tract infection 46
- Respiratory tract neoplasm 21
- Restless legs syndrome 5
- Retinal degeneration 15
- Retinal disease 18
- Retinal Dystrophies 8
- Retinal Neoplasms 4
- Retinal vein occlusion 5
- Retinitis pigmentosa 25
- Retinoblastoma 14
- Retinopathy of prematurity 6
- Retinoschisis 3
- Rett syndrome 8
- Revesz syndrome 7
- Rhabdoid tumor 52
- Rhabdomyosarcoma 68
- Rheumatic Diseases 30
- Rheumatic fever 4
- Rheumatic heart disease 4
- Rheumatoid arthritis 130
- Right ventricular dysfunction 5
- RNA virus infectious disease 8
- Rosacea 7
- Rotator cuff tear 7
- Salivary gland neoplasm 47
- Sandhoff disease 3
- Sarcoidosis 10
- Sarcoma 204
- Sarcopenia 10
- Scabies 3
- Schizophrenia 76
- Schizophrenia spectrum disorder 3
- Sciatica 3
- Sclerosing cholangitis 17
- Sclerosis 7
- Scoliosis 3
- Seasonal allergic rhinitis 9
- Sebaceous adenocarcinoma 4
- Secondary hyperparathyroidism 5
- Seizures 21
- Self-Injurious Behavior 5
- Seminoma 11
- Sensorineural hearing loss 8
- Sepsis 48
- Septic shock 26
- Serous cystadenocarcinoma 6
- Severe combined immunodeficiency 8
- Severe Dengue 4
- Sexual Dysfunctions, Psychological 3
- Sexually transmitted infection 14
- Sezary Syndrome 30
- Shock 9
- Short bowel syndrome 5
- Shy-Drager syndrome 4
- Sickle cell trait 5
- Sickle-cell disease 73
- Signet ring cell adenocarcinoma 4
- Sinonasal undifferentiated carcinoma 7
- Sinus tachycardia 13
- Sjogren's Syndrome 29
- Skin and connective tissue diseases 3
- Skin disease 34
- Skin Diseases, Genetic 7
- Skin neoplasm 50
- Sleep apnea 10
- Sleep Initiation and Maintenance Disorders 20
- Sleep-wake disorder 11
- Small cell carcinoma 9
- Smallpox 3
- Smoking 12
- Smoking cessation 14
- Smoldering Multiple Myeloma 24
- Somatostatinoma 8
- Spasms, Infantile 3
- Spasticity 10
- Spinal cord disease 6
- Spinal cord injury 25
- Spinal cord neoplasm 7
- Spinal dysraphism 3
- Spinal muscular atrophies 12
- Spinal Muscular Atrophies of Childhood 8
- Spinal stenosis 5
- Spinocerebellar ataxia 4
- Spinocerebellar degenerations 4
- Splenomegaly 11
- Spondylarthritis 27
- Sprains and strains 4
- Squamous cell carcinoma 72
- Squamous cell neoplasm 16
- Squamous intraepithelial lesions 4
- Staphylococcal infection 7
- Stargardt disease 14
- Status epilepticus 6
- Stiff-person syndrome 13
- Stillbirth 5
- Stomach neoplasm 340
- Stomach Ulcer 4
- Stomatitis 10
- Stomatognathic disease 4
- Streptococcal infection 3
- Stroke 70
- Strongyloidiasis 3
- Stuttering 3
- Subarachnoid hemorrhage 14
- Subcutaneous T-cell lymphoma 5
- Substance Withdrawal Syndrome 6
- Substance-related disorder 14
- Sudden cardiac death 3
- Sudden sensorineural hearing loss 5
- Suicidal ideation 9
- Suicide 8
- Surgical blood loss 8
- Sweat gland disease 4
- Synovial sarcoma 33
- Synucleinopathies 5
- Syphilis 6
- Syringomyelia 3
- Systemic lupus erythematosus 178
- Systemic mastocytosis 4
- Systemic scleroderma 77
- Systolic heart failure 7
- T cell immunodeficiency primary 10
- T-cell leukemia 3
- T-cell lymphoma 74
- T-cell prolymphocytic leukemia 8
- Tachycardia 17
- Takayasu's arteritis 5
- Tauopathies 10
- Telomeric 22q13 Monosomy Syndrome 3
- Temporomandibular joint pathology 5
- Teratoma 10
- Tertiary lymphoid structure 5
- Testicular germ cell tumor 3
- Testicular Neoplasms 17
- Tetanus 4
- Thalassemia 21
- Thoracic Neoplasms 25
- Thrombocythemia, Essential 43
- Thrombocytopenia 26
- Thrombocytopenic purpura 3
- Thrombocytosis 8
- Thromboembolism 7
- Thrombophilia 4
- Thrombosis 19
- Thrombotic Microangiopathies 6
- Thymoma 26
- Thymus epithelial tumor 11
- Thymus neoplasm 10
- Thyroid cancer, follicular 4
- Thyroid gland disease 14
- Thyroid Hurthle cell carcinoma 5
- Thyroid neoplasm 99
- Tibial Fractures 3
- Tinnitus 12
- Tobacco smoking 4
- Tobacco use 4
- Tobacco use cessation 3
- Tobacco use disorder 9
- Tongue neoplasm 8
- Tonic–clonic seizure 3
- Torticollis 4
- Torulopsis 3
- Tourette syndrome 4
- Toxemia 3
- Tracheal disease 4
- Transitional cell carcinoma 146
- Traumatic brain injury 29
- Tremor 4
- Treponemal Infections 7
- Trichotillomania 4
- Trichuriasis 5
- Trigeminal neuralgia 3
- Triple-negative breast neoplasm 334
- Tuberculosis 48
- Tuberculosis, Lymph Node 6
- Tuberculosis, Meningeal 13
- Tuberous sclerosis 10
- Tumor virus infections 3
- Turcot syndrome 33
- Turner syndrome 6
- Type 2 diabetes 171
- Type-1 diabetes 80
- Ulcer 9
- Ulcer 4
- Ulcerative colitis 99
- Unilateral breast neoplasm 11
- Unstable angina 3
- Urachal adenocarcinoma 5
- Urachal cancer 8
- Urea cycle disorder 3
- Ureteral calculi 5
- Ureteral neoplasm 29
- Urethral neoplasm 23
- Urinary incontinence 6
- Urinary tract infection 15
- Urogenital Diseases 16
- Urogenital neoplasm 38
- Urolithiasis 6
- Urologic Diseases 16
- Urologic Neoplasms 35
- Urticaria 4
- Usher Syndromes 5
- Uterine Cervical Dysplasia 4
- Uterine cervix neoplasm 224
- Uterine disease 4
- Uterine Hemorrhage 3
- Uterine neoplasm 61
- Uveal melanoma 49
- Uveitis 10
- Vaccinia 12
- Vaginal neoplasm 21
- Vaginitis 3
- Vaping 4
- Varicose ulcer 5
- Vascular calcification 4
- Vascular disease 16
- Vascular malformation 9
- Vasculitis 35
- Vaso-occlusive crisis 12
- Vasoplegia 5
- Vector-borne disease 5
- Venezuelan equine encephalitis 3
- Venous thromboembolism 17
- Venous thrombosis 12
- Ventilator-associated pneumonia 5
- Ventricular remodeling 4
- Ventricular tachycardia 4
- Ventriculitis 5
- VEXAS syndrome 3
- Viral hemorrhagic fever 6
- Viral pneumonia 6
- Virus Diseases 26
- Vision disorder 9
- Vitamin D deficiency 4
- Vitiligo 27
- Vomiting 17
- Von Hippel-Lindau disease 5
- Von Willebrand's disease 8
- Von Willebrand's disease 3 4
- Vulvar Lichen Sclerosus 4
- Vulvar neoplasm 32
- Vulvodynia 5
- Vulvovaginal candidiasis 4
- Waldenstrom Macroglobulinemia 51
- Wart 6
- Weight gain 10
- Weight loss 26
- Well-being 10
- Wet Macular Degeneration 7
- Wilms Tumor 37
- Wiskott-Aldrich syndrome 7
- Wound infection 3
- Wounds and Injuries 25
- X-Linked Combined Immunodeficiency Diseases 5
- X-linked disease 8
- Xerostomia 4
Source: Phuturdex analysis of ClinicalTrials.gov data (U.S. National Library of Medicine), updated 30 October 2026.