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Aziende quotate negli USA · aggiornato al 13 novembre 2026
Aziende quotate negli USA
Dati da fonti ufficiali, non è una consulenza finanziaria.
367 aziende quotate negli Stati Uniti (borsa e ticker da SEC EDGAR) che sono sponsor di studi clinici attivi, con la pipeline per fase, le prossime date e i dati SEC, aggiornati al 13 novembre 2026.
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Entra gratis →Le aziende con più farmaci in sviluppo
- AstraZeneca NYSE: AZN · 181 farmaci
- Eli Lilly and Company NYSE: LLY · 144 farmaci
- AbbVie NYSE: ABBV · 116 farmaci
- Bristol-Myers Squibb NYSE: BMY · 109 farmaci
- Pfizer NYSE: PFE · 108 farmaci
- Regeneron Pharmaceuticals Nasdaq: REGN · 77 farmaci
- Sanofi Nasdaq: SNY · 75 farmaci
- Amgen Nasdaq: AMGN · 55 farmaci
- BeOne Medicines Nasdaq: ONC · 53 farmaci
- Gilead Sciences Nasdaq: GILD · 51 farmaci
- Incyte Corporation Nasdaq: INCY · 41 farmaci
- Novo Nordisk A/S NYSE: NVO · 39 farmaci
- Genmab Nasdaq: GMAB · 38 farmaci
- BioNTech SE Nasdaq: BNTX · 37 farmaci
- Jazz Pharmaceuticals Nasdaq: JAZZ · 25 farmaci
- Exelixis Nasdaq: EXEL · 21 farmaci
- Revolution Medicines, Inc. Nasdaq: RVMD · 19 farmaci
- ImmunityBio, Inc. Nasdaq: IBRX · 18 farmaci
- Karyopharm Therapeutics Inc Nasdaq: KPTI · 18 farmaci
- Biogen Nasdaq: BIIB · 16 farmaci
- Kura Oncology, Inc. Nasdaq: KURA · 16 farmaci
- Inhibrx Biosciences, Inc Nasdaq: INBX · 15 farmaci
- Alnylam Pharmaceuticals Nasdaq: ALNY · 14 farmaci
- IDEAYA Biosciences Nasdaq: IDYA · 14 farmaci
Tutte le aziende (A–Z)
- 4D Molecular Therapeutics Nasdaq: FDMT · 3 farmaci
- 60 Degrees Pharmaceuticals LLC Nasdaq: SXTP · 1 farmaco
- AbbVie NYSE: ABBV · 116 farmaci
- AbCellera Biologics Inc. Nasdaq: ABCL · 2 farmaci
- Abeona Therapeutics, Inc Nasdaq: ABEO · 1 farmaco
- Abivax S.A. Nasdaq: ABVX · 1 farmaco
- AC Immune SA Nasdaq: ACIU · 1 farmaco
- ACADIA Pharmaceuticals Inc. Nasdaq: ACAD · 2 farmaci
- Achieve Life Sciences Nasdaq: ACHV · 1 farmaco
- Aclaris Therapeutics, Inc. Nasdaq: ACRS · 1 farmaco
- Acrivon Therapeutics Nasdaq: ACRV · 3 farmaci
- Actinium Pharmaceuticals NYSE: ATNM · 3 farmaci
- Actuate Therapeutics Inc. Nasdaq: ACTU · 7 farmaci
- Acumen Pharmaceuticals Nasdaq: ABOS · 1 farmaco
- Acurx Pharmaceuticals Inc. Nasdaq: ACXP · 1 farmaco
- Adagene Inc Nasdaq: ADAG · 3 farmaci
- ADARx Pharmaceuticals, Inc. Nasdaq: ADRX · 5 farmaci
- ADC Therapeutics S.A. NYSE: ADCT · 6 farmaci
- Agenus Inc. Nasdaq: AGEN · 2 farmaci
- Agios Pharmaceuticals, Inc. Nasdaq: AGIO · 4 farmaci
- Akebia Therapeutics Nasdaq: AKBA · 3 farmaci
- Aligos Therapeutics Nasdaq: ALGS · 3 farmaci
- Alkermes, Inc. Nasdaq: ALKS · 2 farmaci
- Allarity Therapeutics Nasdaq: ALLR · 1 farmaco
- Allogene Therapeutics Nasdaq: ALLO · 6 farmaci
- Alnylam Pharmaceuticals Nasdaq: ALNY · 14 farmaci
- Alterity Therapeutics Nasdaq: ATHE · 1 farmaco
- Altimmune, Inc. Nasdaq: ALT · 1 farmaco
- Alto Neuroscience NYSE: ANRO · 4 farmaci
- Alumis Inc Nasdaq: ALMS · 1 farmaco
- Alzamend Neuro, Inc. Nasdaq: ALZN · 3 farmaci
- Amgen Nasdaq: AMGN · 55 farmaci
- Amneal Pharmaceuticals, LLC Nasdaq: AMRX · 1 farmaco
- Amylyx Pharmaceuticals Inc. Nasdaq: AMLX · 3 farmaci
- AN2 Therapeutics, Inc Nasdaq: ANTX · 1 farmaco
- AnaptysBio, Inc. Nasdaq: ANAB · 1 farmaco
- Annexon, Inc. Nasdaq: ANNX · 1 farmaco
- Annovis Bio Inc. NYSE: ANVS · 2 farmaci
- Apnimed Nasdaq: APMD · 2 farmaci
- Apollomics Inc. Nasdaq: APLM · 1 farmaco
- Aprea Therapeutics Nasdaq: APRE · 1 farmaco
- Aptevo Therapeutics Nasdaq: APVO · 3 farmaci
- Arcus Biosciences, Inc. NYSE: RCUS · 12 farmaci
- Arcutis Biotherapeutics, Inc. Nasdaq: ARQT · 2 farmaci
- Ardelyx Nasdaq: ARDX · 1 farmaco
- argenx Nasdaq: ARGX · 5 farmaci
- ArriVent BioPharma, Inc. Nasdaq: AVBP · 4 farmaci
- Arrowhead Pharmaceuticals Nasdaq: ARWR · 4 farmaci
- ARS Pharmaceuticals, Inc. Nasdaq: SPRY · 1 farmaco
- Artiva Biotherapeutics, Inc. Nasdaq: ARTV · 5 farmaci
- Arvinas Inc. Nasdaq: ARVN · 5 farmaci
- Ascendis Pharma A/S Nasdaq: ASND · 3 farmaci
- Aspen Neuroscience Nasdaq: ASPE · 1 farmaco
- Assembly Biosciences Nasdaq: ASMB · 1 farmaco
- AstraZeneca NYSE: AZN · 181 farmaci
- Atea Pharmaceuticals, Inc. Nasdaq: AVIR · 1 farmaco
- Atossa Therapeutics, Inc. Nasdaq: ATOS · 2 farmaci
- Atrium Therapeutics Nasdaq: RNA · 1 farmaco
- Attovia Therapeutics Inc Nasdaq: ATTO · 2 farmaci
- aTyr Pharma, Inc. Nasdaq: ATYR · 1 farmaco
- Aurinia Pharmaceuticals Inc. Nasdaq: AUPH · 1 farmaco
- Avalyn Pharma Inc. Nasdaq: AVLN · 2 farmaci
- Axsome Therapeutics, Inc. Nasdaq: AXSM · 4 farmaci
- Azitra Inc. NYSE: AZTR · 1 farmaco
- Bambusa Therapeutics Nasdaq: BBTX · 2 farmaci
- Bausch & Lomb Incorporated NYSE: BLCO · 1 farmaco
- Beam Therapeutics Inc. Nasdaq: BEAM · 4 farmaci
- Belite Bio, Inc Nasdaq: BLTE · 1 farmaco
- BeOne Medicines Nasdaq: ONC · 53 farmaci
- Bicara Therapeutics Nasdaq: BCAX · 2 farmaci
- BioAge Labs, Inc. Nasdaq: BIOA · 1 farmaco
- BioCryst Pharmaceuticals Nasdaq: BCRX · 2 farmaci
- Biogen Nasdaq: BIIB · 16 farmaci
- BioLineRx, Ltd. Nasdaq: BLRX · 1 farmaco
- BioMarin Pharmaceutical Nasdaq: BMRN · 7 farmaci
- Biomea Fusion Inc. Nasdaq: BMEA · 1 farmaco
- BioNTech SE Nasdaq: BNTX · 37 farmaci
- BioRestorative Therapies Nasdaq: BRTX · 1 farmaco
- Bioventus LLC Nasdaq: BVS · 1 farmaco
- Black Diamond Therapeutics, Inc. Nasdaq: BDTX · 2 farmaci
- BlossomHill Therapeutics Nasdaq: BLSM · 5 farmaci
- Bolt Biotherapeutics, Inc. Nasdaq: BOLT · 1 farmaco
- Braveheart Bio, Inc. Nasdaq: BRVE · 1 farmaco
- BriaCell Therapeutics Corporation Nasdaq: BCTX · 2 farmaci
- Bright Minds Biosciences Pty Ltd Nasdaq: DRUG · 1 farmaco
- Bristol-Myers Squibb NYSE: BMY · 109 farmaci
- C4 Therapeutics, Inc. Nasdaq: CCCC · 3 farmaci
- Cabaletta Bio Nasdaq: CABA · 3 farmaci
- CAMP4 Therapeutics Corporation Nasdaq: CAMP · 1 farmaco
- Can-Fite BioPharma NYSE: CANF · 2 farmaci
- Candel Therapeutics, Inc. Nasdaq: CADL · 2 farmaci
- Cardiff Oncology Nasdaq: CRDF · 2 farmaci
- Cardiol Therapeutics Inc. Nasdaq: CRDL · 1 farmaco
- Caribou Biosciences, Inc. Nasdaq: CRBU · 4 farmaci
- Cartesian Therapeutics Nasdaq: RNAC · 2 farmaci
- Celcuity Inc Nasdaq: CELC · 5 farmaci
- Celldex Therapeutics Nasdaq: CLDX · 2 farmaci
- Cellectar Biosciences, Inc. Nasdaq: CLRB · 2 farmaci
- Cellectis S.A. Nasdaq: CLLS · 4 farmaci
- Century Therapeutics, Inc. Nasdaq: IPSC · 1 farmaco
- Clearmind Medicine Inc. Nasdaq: CMND · 1 farmaco
- Climb Bio, Inc. Nasdaq: CLYM · 2 farmaci
- CNS Pharmaceuticals, Inc. Nasdaq: CNSP · 1 farmaco
- Cogent Biosciences, Inc. Nasdaq: COGT · 6 farmaci
- Cognition Therapeutics Nasdaq: CGTX · 1 farmaco
- Coherus Oncology, Inc. Nasdaq: CHRS · 7 farmaci
- Colgate Palmolive NYSE: CL · 1 farmaco
- COMPASS Pathways Nasdaq: CMPS · 1 farmaco
- Compass Therapeutics Nasdaq: CMPX · 5 farmaci
- Compugen Ltd Nasdaq: CGEN · 3 farmaci
- Context Therapeutics Inc. Nasdaq: CNTX · 2 farmaci
- Contineum Therapeutics Nasdaq: CTNM · 1 farmaco
- Corcept Therapeutics Nasdaq: CORT · 7 farmaci
- Corvus Pharmaceuticals, Inc. Nasdaq: CRVS · 1 farmaco
- Coya Therapeutics Nasdaq: COYA · 1 farmaco
- Creative Medical Technology Holdings Inc Nasdaq: CELZ · 1 farmaco
- Crescent Biopharma, Inc. Nasdaq: CBIO · 11 farmaci
- CRISPR Therapeutics Nasdaq: CRSP · 4 farmaci
- Cullinan Therapeutics Inc. Nasdaq: CGEM · 10 farmaci
- Cumberland Pharmaceuticals Nasdaq: CPIX · 1 farmaco
- Curis, Inc. Nasdaq: CRIS · 3 farmaci
- Cytokinetics Nasdaq: CYTK · 3 farmaci
- CytomX Therapeutics Nasdaq: CTMX · 5 farmaci
- Damora Therapeutics Nasdaq: DMRA · 2 farmaci
- DBV Technologies Nasdaq: DBVT · 1 farmaco
- Delcath Systems Inc. Nasdaq: DCTH · 5 farmaci
- Denali Therapeutics Inc. Nasdaq: DNLI · 8 farmaci
- Design Therapeutics, Inc. Nasdaq: DSGN · 2 farmaci
- Disc Medicine, Inc Nasdaq: IRON · 3 farmaci
- Dogwood Therapeutics Inc. Nasdaq: DWTX · 1 farmaco
- Dyne Therapeutics Nasdaq: DYN · 2 farmaci
- Edesa Biotech Inc. Nasdaq: EDSA · 1 farmaco
- Edgewise Therapeutics, Inc. Nasdaq: EWTX · 3 farmaci
- Editas Medicine, Inc. Nasdaq: EDIT · 1 farmaco
- Eikon Therapeutics Nasdaq: EIKN · 10 farmaci
- Electra Therapeutics Inc. Nasdaq: ETRA · 1 farmaco
- Eledon Pharmaceuticals Nasdaq: ELDN · 1 farmaco
- Eli Lilly and Company NYSE: LLY · 144 farmaci
- Eloxx Pharmaceuticals, Inc. Nasdaq: ELOX · 1 farmaco
- Enanta Pharmaceuticals, Inc Nasdaq: ENTA · 2 farmaci
- Enliven Therapeutics Nasdaq: ELVN · 11 farmaci
- Ensysce Biosciences Nasdaq: ENSC · 2 farmaci
- Entrada Therapeutics, Inc. Nasdaq: TRDA · 2 farmaci
- Equillium Nasdaq: EQ · 1 farmaco
- Erasca, Inc. Nasdaq: ERAS · 4 farmaci
- Estrella Immunopharma, Inc. Nasdaq: ESLA · 1 farmaco
- Eupraxia Pharmaceuticals Inc. Nasdaq: EPRX · 1 farmaco
- Evommune, Inc. NYSE: EVMN · 1 farmaco
- Exelixis Nasdaq: EXEL · 21 farmaci
- Faeth Therapeutics Nasdaq: FTH · 4 farmaci
- Fate Therapeutics Nasdaq: FATE · 11 farmaci
- FibroBiologics Nasdaq: FBLG · 1 farmaco
- Foghorn Therapeutics Inc. Nasdaq: FHTX · 3 farmaci
- Gain Therapeutics, Inc. Nasdaq: GANX · 1 farmaco
- Galmed Pharmaceuticals Ltd Nasdaq: EOCN · 1 farmaco
- Genelux Corporation Nasdaq: GNLX · 11 farmaci
- Generate Biomedicines Nasdaq: GENB · 5 farmaci
- Genmab Nasdaq: GMAB · 38 farmaci
- Genprex, Inc. Nasdaq: GNPX · 3 farmaci
- Geron Corporation Nasdaq: GERN · 2 farmaci
- Gilead Sciences Nasdaq: GILD · 51 farmaci
- Glaukos Corporation NYSE: GKOS · 2 farmaci
- Grace Therapeutics Inc. Nasdaq: GRCE · 1 farmaco
- Greenwich LifeSciences, Inc. Nasdaq: GLSI · 1 farmaco
- Halozyme Therapeutics Nasdaq: HALO · 1 farmaco
- HCW Biologics Nasdaq: HCWB · 1 farmaco
- Humacyte, Inc. Nasdaq: HUMA · 1 farmaco
- Iambic Therapeutics, Inc Nasdaq: IAM · 1 farmaco
- iBio, Inc. Nasdaq: IBIO · 2 farmaci
- IDEAYA Biosciences Nasdaq: IDYA · 14 farmaci
- Immuneering Corporation Nasdaq: IMRX · 5 farmaci
- Immunic AG Nasdaq: IMUX · 1 farmaco
- ImmunityBio, Inc. Nasdaq: IBRX · 18 farmaci
- Immunome, Inc. Nasdaq: IMNM · 5 farmaci
- Immutep S.A.S. Nasdaq: IMMP · 6 farmaci
- Imunon Nasdaq: IMNN · 6 farmaci
- Incannex Healthcare Ltd Nasdaq: IXHL · 2 farmaci
- Incyte Corporation Nasdaq: INCY · 41 farmaci
- Indaptus Therapeutics, Inc Nasdaq: INDP · 2 farmaci
- Inhibikase Therapeutics Nasdaq: IKT · 1 farmaco
- Inhibrx Biosciences, Inc Nasdaq: INBX · 15 farmaci
- Innate Pharma Nasdaq: IPHA · 3 farmaci
- Inovio Pharmaceuticals Nasdaq: INO · 4 farmaci
- Insmed Incorporated Nasdaq: INSM · 4 farmaci
- Intellia Therapeutics Nasdaq: NTLA · 2 farmaci
- Intensity Therapeutics, Inc. Nasdaq: INTS · 1 farmaco
- Intuitive Surgical Nasdaq: ISRG · 1 farmaco
- Invivyd, Inc. Nasdaq: IVVD · 3 farmaci
- Ionis Pharmaceuticals, Inc. Nasdaq: IONS · 12 farmaci
- Iovance Biotherapeutics, Inc. Nasdaq: IOVA · 5 farmaci
- IRulya Therapeutics Inc. Nasdaq: IRLA · 1 farmaco
- Jade Biosciences, Inc. Nasdaq: JBIO · 2 farmaci
- Janux Therapeutics Nasdaq: JANX · 6 farmaci
- Jazz Pharmaceuticals Nasdaq: JAZZ · 25 farmaci
- Kardigan, Inc. Nasdaq: KARD · 3 farmaci
- Karyopharm Therapeutics Inc Nasdaq: KPTI · 18 farmaci
- Keros Therapeutics, Inc. Nasdaq: KROS · 1 farmaco
- Kiniksa Pharmaceuticals International, plc Nasdaq: KNSA · 1 farmaco
- Kiora Pharmaceuticals, Inc. Nasdaq: KPRX · 1 farmaco
- Kodiak Sciences Inc Nasdaq: KOD · 2 farmaci
- Korro Bio, Inc. Nasdaq: KRRO · 1 farmaco
- Krystal Biotech, Inc. Nasdaq: KRYS · 11 farmaci
- Kura Oncology, Inc. Nasdaq: KURA · 16 farmaci
- Kymera Therapeutics, Inc. Nasdaq: KYMR · 1 farmaco
- Kyntra Bio Nasdaq: KYNB · 2 farmaci
- Kyverna Therapeutics Nasdaq: KYTX · 1 farmaco
- Lantern Pharma Inc. Nasdaq: LTRN · 8 farmaci
- Larimar Therapeutics, Inc. Nasdaq: LRMR · 1 farmaco
- Latigo Biotherapeutics Nasdaq: LTGO · 3 farmaci
- LB Pharmaceuticals Inc. Nasdaq: LBRX · 1 farmaco
- LeonaBio Nasdaq: LONA · 2 farmaci
- Lexeo Therapeutics Nasdaq: LXEO · 3 farmaci
- Lexicon Pharmaceuticals Nasdaq: LXRX · 1 farmaco
- Lipocine Inc. Nasdaq: LPCN · 1 farmaco
- Lycia Therapeutics, Inc. Nasdaq: LYCA · 1 farmaco
- Lyell Immunopharma, Inc. Nasdaq: LYEL · 3 farmaci
- MacroGenics Nasdaq: MGNX · 6 farmaci
- Madrigal Pharmaceuticals, Inc. Nasdaq: MDGL · 1 farmaco
- Maia Biotechnology NYSE: MAIA · 2 farmaci
- Mannkind Corporation Nasdaq: MNKD · 1 farmaco
- MapLight Therapeutics Nasdaq: MPLT · 2 farmaci
- Marker Therapeutics, Inc. Nasdaq: MRKR · 2 farmaci
- Maze Therapeutics Nasdaq: MAZE · 2 farmaci
- MBX Biosciences Nasdaq: MBX · 2 farmaci
- MediciNova Nasdaq: MNOV · 2 farmaci
- MediWound Ltd Nasdaq: MDWD · 2 farmaci
- Milestone Pharmaceuticals Inc. Nasdaq: MIST · 1 farmaco
- Mineralys Therapeutics Inc. Nasdaq: MLYS · 1 farmaco
- Minerva Neurosciences Nasdaq: NERV · 4 farmaci
- MiNK Therapeutics Nasdaq: INKT · 1 farmaco
- Mirum Pharmaceuticals, Inc. Nasdaq: MIRM · 4 farmaci
- Moleculin Biotech, Inc. Nasdaq: MBRX · 1 farmaco
- Monopar Therapeutics Nasdaq: MNPR · 1 farmaco
- Monte Rosa Therapeutics, Inc Nasdaq: GLUE · 3 farmaci
- MoonLake Immunotherapeutics AG Nasdaq: MLTX · 1 farmaco
- Nanobiotix Nasdaq: NBTX · 3 farmaci
- Nasus Pharma NYSE: NSRX · 2 farmaci
- Nektar Therapeutics Nasdaq: NKTR · 1 farmaco
- NervGen Pharma Nasdaq: NGEN · 1 farmaco
- Neurocrine Biosciences Nasdaq: NBIX · 9 farmaci
- Neurogene Inc. Nasdaq: NGNE · 2 farmaci
- NewAmsterdam Pharma Nasdaq: NAMS · 3 farmaci
- NextCure, Inc. Nasdaq: NXTC · 1 farmaco
- Nkarta, Inc. Nasdaq: NKTX · 4 farmaci
- Novo Nordisk A/S NYSE: NVO · 39 farmaci
- NovoCure GmbH Nasdaq: NVCR · 2 farmaci
- NuCana plc Nasdaq: NCNA · 2 farmaci
- Nurix Therapeutics, Inc. Nasdaq: NRIX · 8 farmaci
- Nuvation Bio Inc. NYSE: NUVB · 4 farmaci
- Nuvectis Pharma, Inc. Nasdaq: NVCT · 3 farmaci
- Obsidian Therapeutics, Inc. Nasdaq: OBX · 1 farmaco
- Ocugen Nasdaq: OCGN · 4 farmaci
- Ocular Therapeutix, Inc. Nasdaq: OCUL · 1 farmaco
- Odyssey Therapeutics, Inc. Nasdaq: ODTX · 3 farmaci
- Olema Pharmaceuticals, Inc. Nasdaq: OLMA · 8 farmaci
- Omeros Corporation Nasdaq: OMER · 1 farmaco
- Oncolytics Biotech Nasdaq: ONCY · 8 farmaci
- OPKO Health, Inc. Nasdaq: OPK · 2 farmaci
- Organon and Co NYSE: OGN · 1 farmaco
- ORIC Pharmaceuticals Nasdaq: ORIC · 8 farmaci
- Oruka Therapeutics, Inc. Nasdaq: ORKA · 2 farmaci
- Outlook Therapeutics, Inc. Nasdaq: OTLK · 1 farmaco
- Palatin Technologies, Inc Nasdaq: PTN · 3 farmaci
- Palisade Bio Nasdaq: PALI · 1 farmaco
- Palvella Therapeutics, Inc. Nasdaq: PVLA · 1 farmaco
- Parabilis Medicines, Inc. Nasdaq: PBLS · 5 farmaci
- Pasithea Therapeutics Corp. Nasdaq: KTTA · 1 farmaco
- Perspective Therapeutics NYSE: CATX · 3 farmaci
- Pfizer NYSE: PFE · 108 farmaci
- Phathom Pharmaceuticals, Inc. Nasdaq: PHAT · 1 farmaco
- Pliant Therapeutics, Inc. Nasdaq: PLRX · 2 farmaci
- PMV Pharmaceuticals, Inc Nasdaq: PMVP · 6 farmaci
- Polaryx Therapeutics, Inc. Nasdaq: PLYX · 1 farmaco
- Praxis Precision Medicines Nasdaq: PRAX · 5 farmaci
- Precigen, Inc Nasdaq: PGEN · 3 farmaci
- Prelude Therapeutics Incorporated Nasdaq: PRLD · 5 farmaci
- Prime Medicine, Inc. Nasdaq: PRME · 3 farmaci
- Prokidney Nasdaq: PROK · 1 farmaco
- ProMis Neurosciences, Inc Nasdaq: PMN · 1 farmaco
- ProQR Therapeutics Nasdaq: PRQR · 2 farmaci
- Protagonist Therapeutics, Inc. Nasdaq: PTGX · 1 farmaco
- Protara Therapeutics Nasdaq: TARA · 2 farmaci
- PTC Therapeutics Nasdaq: PTCT · 4 farmaci
- Puma Biotechnology, Inc. Nasdaq: PBYI · 2 farmaci
- Pyxis Oncology, Inc Nasdaq: PYXS · 3 farmaci
- Q32 Bio Inc. Nasdaq: QTTB · 1 farmaco
- Quoin Pharmaceuticals Nasdaq: QNRX · 1 farmaco
- Radiopharm Theranostics, Ltd Nasdaq: RADX · 5 farmaci
- Rapport Therapeutics Inc. Nasdaq: RAPP · 1 farmaco
- Recursion Pharmaceuticals Inc. Nasdaq: RXRX · 3 farmaci
- Regeneron Pharmaceuticals Nasdaq: REGN · 77 farmaci
- REGENXBIO Inc. Nasdaq: RGNX · 3 farmaci
- Rein Therapeutics Nasdaq: RNTX · 1 farmaco
- Relay Therapeutics, Inc. Nasdaq: RLAY · 7 farmaci
- Relmada Therapeutics, Inc. Nasdaq: RLMD · 2 farmaci
- RenovoRx Nasdaq: RNXT · 1 farmaco
- Retension Pharmaceuticals. Inc. Nasdaq: RTSN · 1 farmaco
- Revolution Medicines, Inc. Nasdaq: RVMD · 19 farmaci
- Rezolute Nasdaq: RZLT · 1 farmaco
- Rhythm Pharmaceuticals, Inc. Nasdaq: RYTM · 3 farmaci
- Rigel Pharmaceuticals Nasdaq: RIGL · 3 farmaci
- Rocket Pharmaceuticals Inc. Nasdaq: RCKT · 3 farmaci
- SAb Biotherapeutics, Inc. Nasdaq: SABS · 1 farmaco
- Sagimet Biosciences Inc. Nasdaq: SGMT · 2 farmaci
- Sana Biotechnology Nasdaq: SANA · 2 farmaci
- Sanofi Nasdaq: SNY · 75 farmaci
- Sarepta Therapeutics, Inc. Nasdaq: SRPT · 4 farmaci
- Satellos Bioscience, Inc. Nasdaq: MSLE · 2 farmaci
- Savara Inc. Nasdaq: SVRA · 1 farmaco
- Seaport Therapeutics Nasdaq: SPTX · 1 farmaco
- Sellas Life Sciences Group Nasdaq: SLS · 4 farmaci
- Septerna, Inc. Nasdaq: SEPN · 1 farmaco
- Serina Therapeutics NYSE: SER · 1 farmaco
- Shattuck Labs, Inc. Nasdaq: STTK · 1 farmaco
- SIGA Technologies Nasdaq: SIGA · 1 farmaco
- Silence Therapeutics plc Nasdaq: SLN · 1 farmaco
- Skye Bioscience, Inc. Nasdaq: SKYE · 2 farmaci
- Solid Biosciences Inc. Nasdaq: SLDB · 4 farmaci
- Spruce Biosciences Nasdaq: SPRB · 1 farmaco
- Spyre Therapeutics, Inc. Nasdaq: SYRE · 5 farmaci
- Stoke Therapeutics, Inc Nasdaq: STOK · 1 farmaco
- Summit Therapeutics Nasdaq: SMMT · 4 farmaci
- Sutro Biopharma, Inc. Nasdaq: STRO · 3 farmaci
- Syndax Pharmaceuticals Nasdaq: SNDX · 3 farmaci
- Tango Therapeutics, Inc. Nasdaq: TNGX · 11 farmaci
- Tarsus Pharmaceuticals, Inc. Nasdaq: TARS · 3 farmaci
- Taysha Gene Therapies, Inc. Nasdaq: TSHA · 1 farmaco
- Tectonic Therapeutic Nasdaq: TECX · 1 farmaco
- Tempest Therapeutics Nasdaq: TPST · 3 farmaci
- Tenax Therapeutics, Inc. Nasdaq: TENX · 1 farmaco
- Tenaya Therapeutics Nasdaq: TNYA · 2 farmaci
- TG Therapeutics, Inc. Nasdaq: TGTX · 2 farmaci
- Theriva Biologics SL NYSE: TOVX · 3 farmaci
- Tiziana Life Sciences LTD Nasdaq: TLSA · 1 farmaco
- TransCode Therapeutics Nasdaq: RNAZ · 1 farmaco
- Travere Therapeutics, Inc. Nasdaq: TVTX · 2 farmaci
- TRex Bio, Inc. Nasdaq: TRXB · 1 farmaco
- TriSalus Life Sciences, Inc. Nasdaq: TLSI · 1 farmaco
- TScan Therapeutics, Inc. Nasdaq: TCRX · 9 farmaci
- TuHURA Biosciences, Inc. Nasdaq: HURA · 1 farmaco
- Turn Therapeutics Nasdaq: TTRX · 1 farmaco
- Tvardi Therapeutics, Incorporated Nasdaq: TVRD · 4 farmaci
- Tyra Biosciences, Inc Nasdaq: TYRA · 4 farmaci
- Ultragenyx Pharmaceutical Inc Nasdaq: RARE · 6 farmaci
- United Therapeutics Nasdaq: UTHR · 2 farmaci
- Upstream Bio Inc. Nasdaq: UPB · 1 farmaco
- UroGen Pharma Ltd. Nasdaq: URGN · 2 farmaci
- Vanda Pharmaceuticals Nasdaq: VNDA · 9 farmaci
- Vera Therapeutics, Inc. Nasdaq: VERA · 1 farmaco
- Veradermics, Inc. NYSE: MANE · 1 farmaco
- Verastem, Inc. Nasdaq: VSTM · 13 farmaci
- Vericel Corporation Nasdaq: VCEL · 1 farmaco
- Verrica Pharmaceuticals Inc. Nasdaq: VRCA · 3 farmaci
- Veru Inc. Nasdaq: VERU · 2 farmaci
- Viatris Inc. Nasdaq: VTRS · 1 farmaco
- Viking Therapeutics, Inc. Nasdaq: VKTX · 1 farmaco
- Vir Biotechnology, Inc. Nasdaq: VIR · 6 farmaci
- Vogenx, Inc. Nasdaq: VOGX · 1 farmaco
- Vor Biopharma Nasdaq: VOR · 1 farmaco
- Voyager Therapeutics Nasdaq: VYGR · 2 farmaci
- vTv Therapeutics Nasdaq: VTVT · 1 farmaco
- Whitehawk Therapeutics, Inc. Nasdaq: WHWK · 3 farmaci
- X4 Pharmaceuticals Nasdaq: XFOR · 1 farmaco
- XBiotech, Inc. Nasdaq: XBIT · 3 farmaci
- Xencor, Inc. Nasdaq: XNCR · 7 farmaci
- Xenon Pharmaceuticals Inc. Nasdaq: XENE · 1 farmaco
- Zura Bio Inc Nasdaq: ZURA · 1 farmaco
Fonti: SEC EDGAR (borsa, ticker, documenti e dati di bilancio XBRL, opere del governo USA); ClinicalTrials.gov (U.S. National Library of Medicine), FDA (Drugs@FDA, Orange e Purple Book, farmaci orfani) ed EMA, dati elaborati da Phuturdex e aggiornati al 13 novembre 2026. Studi attivi = in reclutamento o in corso, fasi I–III. Lo sponsor è quello dichiarato da ogni studio; i nomi delle aziende sono collegati alla SEC solo quando coincidono, a parte la forma giuridica. Brevetti, esclusive, approvazioni e pareri sono attribuiti all’azienda solo se ne è titolare nel registro ufficiale. Nessun prezzo o grafico di borsa. Fanno fede solo le fonti ufficiali.