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Drugs in development · updated 30 October 2026

Cemdisiran: clinical trials and development status

FDA substance registryNot approved in the USNo EMA authorisationEstimated launch Dec 2027 – Oct 2028 (Phuturdex estimate)

As of 30 October 2026 Cemdisiran is in 5 active clinical trials (recruiting or ongoing, phases I–III) for 4 diseases. The most advanced phase is III.

5Active trials
IIIMost advanced phase
4Diseases studied

Summary updated every week · data as of 30 October 2026. In Phuturdex you can follow Cemdisiran and get an email at every change or safety alert.

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Diseases studied

For each disease: the drug’s most advanced phase and active trials, with the reference trial on ClinicalTrials.gov.

DiseaseMost advanced phaseActive trialsReference trial
Paroxysmal nocturnal hemoglobinuriaIII3NCT05744921
Geographic atrophyIII1NCT06541704
Macular degenerationIII1NCT06541704
Myasthenia gravisIII1NCT05070858

Everything on Cemdisiran

In Phuturdex you get every trial with sponsors, countries and dates, development events, FDA and EMA approvals, patents and exclusivities, orphan designations and safety alerts, with PDF and Excel export. Free until 31 March 2027.

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Source: Phuturdex analysis of ClinicalTrials.gov (U.S. National Library of Medicine), FDA and EMA data, updated 30 October 2026. Active trials = recruiting or ongoing, phases I–III. Diseases are those named by each trial (NLM MeSH terms). The estimated launch, when shown, is a Phuturdex calculation described on the Method page, not official data.

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