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Drugs in development · updated 30 October 2026

Pacritinib: clinical trials and development status

Other names and codes: Vonjo

FDA verified identityApproved in the US (FDA)

As of 30 October 2026 Pacritinib is in 22 active clinical trials (recruiting or ongoing, phases I–III) for 30 diseases. The most advanced phase is III.

22Active trials
IIIMost advanced phase
30Diseases studied

Summary updated every week · data as of 30 October 2026. In Phuturdex you can follow Pacritinib and get an email at every change or safety alert.

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Diseases studied

For each disease: the drug’s most advanced phase and active trials, with the reference trial on ClinicalTrials.gov.

DiseaseMost advanced phaseActive trialsReference trial
MyelofibrosisIII8NCT03165734
AnemiaIII2NCT03165734
Bone marrow diseaseIII2NCT03165734
Blood platelet diseaseIII1NCT03165734
Hematologic DiseasesIII1NCT03165734
Hemorrhagic diseaseIII1NCT03165734
SplenomegalyIII1NCT03165734
Myeloproliferative disordersII4NCT04282187
Chronic myelomonocytic leukemiaII3NCT07033598
Myelodysplastic SyndromesII3NCT06782373
Lymphoproliferative disordersII2NCT06052618
Polycythemia veraII2NCT04282187
Thrombocythemia, EssentialII2NCT04282187
ThrombocytopeniaII2NCT07447817
VEXAS syndromeII2NCT06782373
Acute monocytic leukemiaII1NCT04282187
Acute myeloid leukemiaII1NCT04282187
Aplastic anemiaI–II1NCT06303193
Breast neoplasmI–II1NCT04520269
FibrosisI–II1NCT05531786
Graft-versus-host diseaseI–II1NCT05531786
Hematologic neoplasmII1NCT06782373
InflammationI–II1NCT05531786
LymphomaII1NCT06986174
Lymphoma, B-Cell, Marginal ZoneII1NCT06986174
Myelodysplastic–myeloproliferative diseasesII1NCT04282187
Prostatic NeoplasmsII1NCT07226713
Refractory anemia with excess of blastsI–II1NCT06303193
Waldenstrom MacroglobulinemiaII1NCT06986174
Mantle cell lymphomaI1NCT06675123

Everything on Pacritinib

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Source: Phuturdex analysis of ClinicalTrials.gov (U.S. National Library of Medicine), FDA and EMA data, updated 30 October 2026. Active trials = recruiting or ongoing, phases I–III. Diseases are those named by each trial (NLM MeSH terms). The estimated launch, when shown, is a Phuturdex calculation described on the Method page, not official data.

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